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Rare Disease Innovation and Partnering Summit 2019

13/06/2019 - 14/06/2019

Connect with key stakeholders, and propel curative progress, orphan product success and patient advocacy at the Rare Disease Innovation and Partnering Summit, June 13–14, 2019 at the Boston Marriott Long Wharf in Boston, MA, co-produced by CBI and EBD Group, with support from the Alliance for Regenerative Medicine, Global Genes and MassBio.

As genomics and advanced diagnostics expand our understanding of rare diseases, so too does the scope of impact expand. More than 30 million Americans live with a rare disease. While the industry has seen growth and heightened focus around the pursuit of orphan products and rare therapies, we’ve only scratched the surface.

The event is a platform designed to increase chances of therapeutic success for drug developers, patient groups and investors within the rare disease marketplace. Business brings breakthroughs. Breakthroughs can transform lives.

Take a deep dive into the critical and evolving topics impacting you today and hear from industry thought leaders and patient advocates who have designed and led innovative approaches to complex challenges in driving curative progress. Program tracks include Patient-Driven Progress, Reimbursement and Access, New Launch and Commercialization, and Partnering and Investment, with regulatory and policy updates and panels on real-life case examples.

Hear additional perspectives and insights from 50+ leaders at companies such as Aegerion Pharmaceuticals, Alliance for Regenerative Medicine, Asklepios BioPharmaceuticals, Athersys, Bexion Pharmaceuticals, BioMarin, bluebird bio, Blueprint Medicines, Boston Children’s Hospital, Cotinga Pharmaceuticals, Cure CMT4J, Cydan II Inc., EveryLife Foundation for Rare Diseases, Geisinger, Global Genes, Horizon Pharma, Intercept Pharmaceuticals, Jackson Lab, Massachusetts General Hospital, MDA, Pfizer, Rare Access Action Project, Recordati Rare Diseases, Recursion Pharmaceutical, Sobi, Syros Pharmaceuticals, Tufts University School of Medicine, Xontogeny and more. The conference also features partneringONE®, the gold standard partnering platform enabling delegates to efficiently identify, meet and network with companies from across the life science value chain.

Registration Specialist
Matt Hannon
CBI T: +1 339 298 2157

EBD Group
T: +1 339 298 2157


Boston Marriott Long Wharf
296 State Street
Boston, 02109 United States
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