News and Trends 1 Sep 2022 Sanofi’s first treatment in the U.S. approved for adults and children with ASMD …and Drug Administration (FDA). Adults and children with non-central nervous system (non-CNS) manifestations of acid sphingomyelinase deficiency (ASMD) can now take healthcare company Sanofi’s Xenpozyme (olipudase alfa-rpcp) – the first therapy… September 1, 2022 - 4 minutesmins - By Liza Laws Share WhatsApp Twitter Linkedin Email
News and Trends 13 Dec 2016 European Pharma closes 2016 by launching new Biotech Startups …by investing in a pair of new ventures. Bayer and Versant have invested $225M to launch BlueRock Therapeutics, which will focus on CNS and cardiovascular diseases. This comes as Novartis… December 13, 2016 - 2 minutesmins - By Evelyn Warner Share WhatsApp Twitter Linkedin Email
Best in Biotech 21 Oct 2025 Seven of the top biotech companies to know about in South San Francisco …to improving mental health by developing an innovative pipeline of central nervous system (CNS) medications to try and establish a new standard of care in the treatment of anxiety, depression,… October 21, 2025 - 9 minutesmins - By Willow Shah-Neville Share WhatsApp Twitter Linkedin Email
Best in Biotech 28 Nov 2024 Six antisense oligonucleotide companies shaping the future of genetic medicine …MicroRNA expression or function is significantly altered in numerous diseases including cancer and fibrosis, as well as in central nervous system (CNS), metabolic, and inflammatory disorders. Regulus is currently focused… November 28, 2024 - 10 minutesmins - By Willow Shah-Neville Share WhatsApp Twitter Linkedin Email
Best in Biotech 16 Dec 2024 10 biotech companies to watch in 2025 …designation for Rett syndrome, fragile X syndrome, and infantile spasms A neuroscience company, Anavex Life Sciences, is developing small-molecule treatments for CNS disorders like Alzheimer’s disease, Parkinson’s disease, and Rett… December 16, 2024 - 14 minutesmins - By Willow Shah-Neville Share WhatsApp Twitter Linkedin Email
Best in Biotech 19 Aug 2025 10 biotech companies you should know about in Spain …for the treatment of cALD Minoryx Therapeutics is focused on the discovery and development of novel therapies for severe, orphan genetic diseases of the central nervous system (CNS) with high… August 19, 2025 - 16 minutesmins - By Willow Shah-Neville Share WhatsApp Twitter Linkedin Email
News and Trends 21 Sep 2022 NodThera reveals positive results for inflammasome inhibitors …profile and the potential for once-a-day dosing. The results collectively support further development and clinical evaluation in a range of central nervous system (CNS) and peripheral inflammatory diseases. “We are… September 21, 2022 - 2 minutesmins - By Jim Cornall Share WhatsApp Twitter Linkedin Email
News and Trends 31 May 2022 Award to help NRG Therapeutics develop new Parkinson’s and Motor Neuron Disease treatments …to date from exploring mPTP inhibitors as novel therapeutic treatments, has been the poor central nervous system (CNS) penetration of known mPTP inhibitors. “NRG’s small molecules are the first orally… May 31, 2022 - 3 minutesmins - By Jim Cornall Share WhatsApp Twitter Linkedin Email
Best in Biotech 29 Feb 2024 6 biotech companies making a difference in pediatric care …a “kids-first” biotech company, is harnessing CAR-T cell technology for tumors in the central nervous system (CNS), with an initial focus on pediatric indications. BrainChild Bio has been granted an… February 29, 2024 - 8 minutesmins - By Willow Shah-Neville Share WhatsApp Twitter Linkedin Email
Best in Biotech 4 Apr 2023 6 biotechs that have stepped into the protein degradation space …(CNS) diseases, the platform successfully underwent preclinical trials to exhibit its efficacy – its ability to penetrate the blood-brain barrier. Depending on the disorder, PROTAC can be administered intravenously and… April 4, 2023 - 7 minutesmins - By Roohi Mariam Peter Share WhatsApp Twitter Linkedin Email
Best in Biotech 4 Nov 2022 Get to know 15 of the best biotech companies in Paris …in 2009 by Karen Aiach after her daughter was diagnosed with Sanfilippo syndrome, a rare disease of the central nervous system (CNS) with no treatment available beyond palliative care. Lysogene… November 4, 2022 - 11 minutesmins - By Omnia Ibrahim Share WhatsApp Twitter Linkedin Email
News and Trends 3 Jan 2023 Newron announces interim results from treatment-resistant schizophrenia trial …of the central and peripheral nervous system (CNS). The results demonstrated a continued improvement in TRS symptoms after six months of treatment with evenamide, as well as a substantially greater… January 3, 2023 - 4 minutesmins - By Jim Cornall Share WhatsApp Twitter Linkedin Email