cystic fibrosis Archives

In Depth 9 Apr 2025

Cystic fibrosis: is the next blockbuster a gene therapy?

Learn about the biotechs progressing their gene therapies for cystic fibrosis and why it might just be the breakthrough that patients need.

April 9, 2025 - 10 minutesmins - By Roohi Mariam Peter

Best in Biotech 7 Nov 2024

Cystic fibrosis: Five biotechs breathing life into the therapeutic space

In this article, we take a look at five biotechs developing potentially transformative medicines to treat this genetic disease.

November 7, 2024 - 8 minutesmins - By Roohi Mariam Peter

In Depth 2 May 2024

New treatments for cystic fibrosis: boosting life expectancy

Discover how cystic fibrosis treatments are extending life expectancy, with recent advancements set to increase it by 75% by next year.

May 2, 2024 - 7 minutesmins - By Roohi Mariam Peter

In Depth 4 Apr 2024

Seven diseases CRISPR technology could cure

Here are some of the diseases that scientists aim to tackle using CRISPR technology, testing its possibilities and limits as a medical tool.

April 4, 2024 - 11 minutesmins - By Clara Rodríguez Fernández

News and Trends 20 Jun 2023

Anoat raises funds to tackle cystic fibrosis

Anoat Therapeutics, a French preclinical stage biotechnology company specialized in cystic fibrosis (CF), has raised €2 million ($2.17 million) in seed funding from AdBio partners. Anoat will use the funds to conduct additional in vivo and in vitro pharmacology assessments and select a lead candidate. Anoat Therapeutics’ goal is to bring a transformative and mutation-agnostic […]

June 20, 2023 - 3 minutesmins - By Jim Cornall

News and Trends 16 Mar 2023

Inspire Biotherapeutics launches to target lung diseases through gene therapy

Inspire Biotherapeutics Inc., an emerging Canadian biotech company with a mission to create gene therapies for monogenic and acquired diseases of the lung, is set to move its novel lung tropic AAV gene therapy into clinical validation. The AAVenger platform has demonstrated transduction and long-term expression in lung tissue without impact on other tissue types […]

March 16, 2023 - 2 minutesmins - By Jim Cornall

News and Trends 15 Mar 2023

Nanite receives funding to deliver genetic therapies to the lungs

Nanite Inc. has announced an investment from the Cystic Fibrosis Foundation of up to $2 million to develop gene delivery technologies for the lung. This builds on the $6 million seed financing recently announced by the company. One of the most significant challenges in developing new therapies for patients with cystic fibrosis is effective drug […]

March 15, 2023 - 2 minutesmins - By Jim Cornall

News and Trends 11 Jan 2023

Renexxion goes to FDA with cystic fibrosis drug

Renexxion Ireland Limited has opened an investigational new drug (IND) application with the U.S Food and Drug Administration (FDA) for naronapride for the treatment of GI motility disorders in patients with cystic fibrosis (CF). This is a first step towards conducting clinical trials of the drug candidate in CF patients. Naronapride, post approval, could be […]

January 11, 2023 - 2 minutesmins - By Jim Cornall

News and Trends 14 Nov 2022

A biotech boom manifesting real results in rare pediatric diseases

By Bob Coughlin, managing director, life sciences, JLL For the last two years, the pandemic has resulted in the explosive growth in life sciences. The world watched in awe and anticipation as biotech successfully raced to develop vaccines, therapeutics and diagnostics for Covid-19. It has been a good moment for an industry that deserves such […]

November 14, 2022 - 5 minutesmins - By External Contributor

News and Trends 2 Aug 2022

FDA gives ok to Krystal Biotech cystic fibrosis clinical trial

U.S. company Krystal Biotech is set to start a clinical trial for cystic fibrosis after the United States Food and Drug Administration (FDA) accepted its investigational new drug (IND) application. The gene therapy company will be evaluating KB407, a modified HSV-1 vector carrying two copies of the cystic fibrosis transmembrane conductance regulator (CFTR) gene to […]

August 2, 2022 - 3 minutesmins - By Jim Cornall

News and Trends 22 Jun 2022

Cystic fibrosis in the crosshairs as Carbon Biosciences launches with $38M funding

Carbon Biosciences, a Longwood Fund founded biotech company developing parvovirus-derived gene therapies, has launched with $38 million of financing led by Agent Capital. Agent is joined by Longwood Fund, Astellas Venture Management LLC, the Cystic Fibrosis Foundation, Solasta Ventures, University of Tokyo Innovation Platform (UTokyoIPC), and Camford Capital. Massachusetts-based Carbon is harnessing novel parvovirus vectors […]

June 22, 2022 - 3 minutesmins - By Jim Cornall

Expert Advice 27 May 2020

Why Listening to Patient Organizations is Key in Drug Development

As the biotech industry flourishes and therapies become more targeted and personalized, the need for drug developers to interact with patients is increasing as well. While patient organizations took a backseat in the past, they are continuously gaining importance in drug development today. Nowadays, talking with patient organizations has become paramount for successful drug development, […]

May 27, 2020 - 11 minutesmins - By Larissa Warneck-Silvestrin

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cystic fibrosis

Cystic fibrosis: is the next blockbuster a gene therapy?

Cystic fibrosis: Five biotechs breathing life into the therapeutic space

New treatments for cystic fibrosis: boosting life expectancy

Seven diseases CRISPR technology could cure

Anoat raises funds to tackle cystic fibrosis

Inspire Biotherapeutics launches to target lung diseases through gene therapy

Nanite receives funding to deliver genetic therapies to the lungs

Renexxion goes to FDA with cystic fibrosis drug

A biotech boom manifesting real results in rare pediatric diseases

FDA gives ok to Krystal Biotech cystic fibrosis clinical trial

Cystic fibrosis in the crosshairs as Carbon Biosciences launches with $38M funding

Why Listening to Patient Organizations is Key in Drug Development

Subscribe to our newsletter to get the latest biotech news!

Illuminating biotech in the City of Light: Inside Paris’s thriving ecosystem

ASCO 2025: key highlights in cancer therapeutics

New report: Artificial intelligence and the future of antibody discovery

Stem cell therapy: a potential cure for hearing loss?

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

Illuminating biotech in the City of Light: Inside Paris’s thriving ecosystem

ASCO 2025: key highlights in cancer therapeutics

New report: Artificial intelligence and the future of antibody discovery

Stem cell therapy: a potential cure for hearing loss?

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

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