5 advancements in kidney disease research over the past year
Prevalent in millions of people across the globe, kidney diseases manifest through various symptoms like…
March 9, 2023 - 7 minutes
FDA
Interview: how has the first gene therapy for hemophilia B transformed research?
Hemophilia B, a rare disease that affects more than 230,000 people worldwide is caused by…
March 3, 2023 - 8 minutes
Orphan drug designation for Laevoroc metabolic immune checkpoint inhibitor
Laevoroc Immunology, a privately-owned, Swiss oncology development company, has announced that the U.S. Food and…
March 3, 2023 - 3 minutes
Let’s Take a Closer Look at 7 Autoimmune Diseases Biotechs are Fighting to Treat
While we mostly think of disease as being caused by bacteria or viruses, an illness…
March 3, 2023 - 8 minutes
Sanofi hemophilia drug gets FDA approval
The U.S. Food and Drug Administration (FDA) has approved Sanofi's ALTUVIIIO [Antihemophilic Factor (Recombinant), Fc-VWF-XTEN…
February 24, 2023 - 4 minutes
Depression trial gets green light
Beckley Psytech Ltd has received investigational new drug (IND) approval from the U.S. Food and…
February 23, 2023 - 3 minutes
FDA approves alpha-mannosidosis drug
Chiesi Global Rare Diseases, a business unit of Chiesi Farmaceutici S.p.A., an international research-focused healthcare…
February 21, 2023 - 3 minutes
FDA approves GSK drug for recurrent or advanced mismatch repair-deficient endometrial cancer
GSK plc says the US Food and Drug Administration (FDA) has given full approval for…
February 10, 2023 - 3 minutes
Rocket Pharmaceuticals receives FDA RMAT designation for Danon disease gene therapy treatment
Rocket Pharmaceuticals, Inc says the U.S. Food and Drug Administration (FDA) has granted regenerative medicine…
February 10, 2023 - 3 minutes
Endogena Therapeutics retinitis pigmentosa treatment gets FDA fast track designation
The US Food and Drug Administration (FDA) has designated the investigation of Endogena Therapeutics’ EA-2353…
February 7, 2023 - 2 minutes
Genoscience Pharma receives orphan drug designation for hepatocellular carcinoma drug
Genoscience Pharma has announced that its lead candidate, ezurpimtrostat, a PPT-1 (Palmitoyl Protein Thioesterase-1) inhibitor,…
February 3, 2023 - 3 minutes
Stemline Therapeutics’ breast cancer treatment approved
The Menarini Group, an Italian pharmaceutical and diagnostics company, says that the U.S. Food and…
January 31, 2023 - 3 minutes
