EMA designates uniQure’s gene therapy for hemophilia a priority
Following a Breakthrough Designation from the FDA earlier this year, the Dutch biotech has scored the European equivalent…
April 25, 2017 - 3 minutes
Hemophilia
It’s Global Rare Disease Day! What Cures is Biotech Cooking Up?
We've compiled a list of some of the latest advances of biotech in the field…
February 28, 2017 - 5 minutes
The FDA gives Fast Track Priority to uniQure’s Hemophilia B Gene Therapy
UniQure has received Breakthrough Therapy Designation from the FDA, granting fast track to its gene therapy…
January 30, 2017 - 2 minutes
After a Rough Year, uniQure CMO discusses a Comeback
Last year was a bad year for biotech as an industry, but it was particularly…
January 9, 2017 - 4 minutes
UPDATE: UniQure keeps afloat with a New CEO and More Clinical Data
UniQure's gene therapy for Hemophilia B is performing well in clinical trials, but the company faces…
December 20, 2016 - 3 minutes
“We are Pioneering Cell Therapy to Cure NASH and Fibrotic Disease”
Promethera is collecting cash to fuel its liver disease program that revolves around HepaStem. I…
November 21, 2016 - 7 minutes
UniQure takes an axe to its Pipeline and Workforce in new R&D Strategy
UniQure just announced a new R&D plan designed to save up to €27M over the…
November 17, 2016 - 2 minutes
RNAi Therapy is Back: Sanofi is firmly on board to treat Hemophilia
Sanofi Genzyme is offering Alnylam up to €93M ($100M) to co-develop and launch a revolutionary RNAi therapy…
November 15, 2016 - 2 minutes
Roche hits a Speed Bump on the way to a Hemophilia Cure
The Swiss pharma is gearing up for a battle with Novo Nordisk in Hemophilia, but…
November 4, 2016 - 4 minutes
Gene Therapy for severe Hemophilia has new Phase I/II Results
uniQure has new data from the Phase I/II trial of its gene therapy for Hemophilia…
July 29, 2016 - 3 minutes
Rare Disease Biopharma can now sell Hemophilia treatment across whole of EU
Sobi has received market approval by the European Comission for Alprolix, a long-duration protein therapy…
May 17, 2016 - 2 minutes
Global Hemophilia AID project achieves first milestone with donations from Swedish Biotech
The Hemophilia Aid Program has just touched down the first batch of treatments in its…
October 13, 2015 - 3 minutes
