Pompe disease news - the latest biotech news from Labiotech.eu

Home Pompe disease

Latest Posts

acid alpha-glucosidase GAA

News and Trends 9 Jan 2023

Selecta and Astellas sign LOPD treatment agreement

Selecta Biosciences, Inc. and Astellas Pharma Inc. have announced an exclusive licensing and development agreement for IdeXork (Xork). Xork is being studied as a potential next generation immunoglobulin G (IgG)…

January 9, 2023 - 3 minutesmins - By Jim Cornall

glycogen

News and Trends 10 Aug 2022

Aro Biotherapeutics gets FDA orphan drug designation for treatment of Pompe Disease

Aro Biotherapeutics says the U.S. Food and Drug Administration (FDA) has granted Orphan Drug Designation to ABX1100, an investigational Centyrin-siRNA conjugate that targets the Gys1 gene in the muscle, for…

August 10, 2022 - 2 minutesmins - By Jim Cornall

shutterstock pompe disease

News and Trends 27 Jun 2022

Trial for adults with late onset Pompe disease halted due to serious adverse event

The US Food and Drug Administration (FDA) has placed a clinical hold on a trial being run for Astrellas Pharma Inc after one of the participants had a serious adverse…

June 27, 2022 - 3 minutesmins - By Liza Laws

Beyond Biotech - the podcast from Labiotech

View More

Newsletter Signup - Sidebar

"*" indicates required fields

Want to advertise with us?

Reach us here!

Got a news story for us?

Send it to us here