In Depth 18 Apr 2023
Gene therapy: a powerful tool for hemophilia B?
The approval of HEMGENIX, the first-ever gene therapy for hemophilia B, by the U.S. Food and Drug Administration (FDA) followed…
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News and Trends 28 Feb 2023
European Commission approves first gene therapy for hemophilia B
The European Commission has approved the first gene therapy for the treatment of hemophilia B developed by biotech company CSL…
News and Trends 24 Nov 2022
Gene therapy approval “game changer” in hemophilia B treatment
The approval of CSL's gene therapy Hemgenix has ushered in a new era for hemophilia B treatment. With the addition…
Best in Biotech 20 Dec 2021
The Billion-Euro European Biotech Companies in 2022
Here’s a list of the public European biotech companies that are worth more than a billion euros in 2022. European…
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Best in Biotech 2 Sep 2021
The top 15 biotech companies to find in the Netherlands
The Netherlands has established itself as a biotech and life sciences hub, possessing leading academic and research institutions and an…
Best in Biotech 28 Dec 2020
A Year to Remember: The Biggest European Biotech News in 2020
The Covid-19 pandemic caused huge disruption for European biotech in 2020, but the industry pulled through. Let’s look back at…
News and Trends 17 Dec 2020
Covid-19 Leaves Lasting Impact on Hematology at ASH 2020 Conference
Under the heavy shadow of the Covid-19 pandemic, last week’s annual conference of the American Society of Hematology (ASH) displayed…
News and Trends 26 Jun 2020
CSL Behring Nabs UniQure’s Hemophilia Gene Therapy for up to €1.8B
Big pharma CSL Behring will pay the Dutch gene therapy developer uniQure an upfront of €400M for the global…
News and Trends 14 May 2019
First Potential Gene Therapy for Hemophilia B Restores Blood Clotting in Phase II
A gene therapy developed by the Dutch biotech uniQure increased the activity of a blood clotting protein enough to stop…
News and Trends 23 Jan 2019
Update: The FDA Green-lights Clinical Trials for Huntington’s Disease Gene Therapy
Update (23/01/2019): The FDA has given uniQure regulatory clearance to begin a phase I/II trial of its gene therapy for…
News and Trends 6 Dec 2018
Update: Liver Gene Therapy 8 Times Stronger Than Usual
Update (06/12/2018): uniQure has incorporated Synpromics' strong liver promoter into a preclinical gene therapy candidate for treating hemophilia A. Published…
News and Trends 3 May 2018
World’s First Gene Therapy Developer Raises $128M for Hemophilia and Huntington’s
uniQure has raised a substantial public offering on the NASDAQ. The funding could help the Dutch biotech advance two new gene…
More News! 28 Feb 2018
Could A More Precise CRISPR/Cas9 System Treat Huntington’s Disease?
Polish researchers tested a new variant of CRISPR/Cas9 that increases the gene-editing system's precision in targeting specific DNA sequences, such…
News and Trends 28 Feb 2018
Like Finding a Needle in a Haystack: How Are Biotechs Fighting Rare Diseases?
Rare diseases affect fewer than 1 in 2,000 people in Europe and less than 200,000 Americans at any given time.…
Best in Biotech 27 Dec 2017
The Biggest Biotech News of 2017: What Happened This Year?
Still catching up on news? We've picked out the most exciting things that happened besides clinical results and finance. Here's…
News and Trends 19 Dec 2017
This Gene Therapy for Hemophilia Can Reduce Bleeding by 70%
UniQure has published clinical data revealing that its gene therapy for hemophilia B is effective for years and lets patients…
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In Depth 28 Nov 2017
Reviewing Gene Therapy: How Close is Biotech to Genetic Cures?
Over 10,000 human diseases are caused by exactly one faulty gene. Gene therapy promises to fix each of them. Here's a…
News and Trends 2 Nov 2017
Close to Launching Gene Therapy, Dutch Biotech Raises Over $91M on the Nasdaq
Update (2/11/2017): uniQure has closed its public offering raising over $91m (€78M) on the Nasdaq, taking advantage of a massive stock jump…
News and Trends 19 Oct 2017
Dutch Biotech plans Pivotal Clinical Trial with First Gene Therapy for Hemophilia
uniQure is getting ready to start a Phase III clinical trial in 2018 with a new version of its gene…
Best in Biotech 26 Sep 2017
These Three Fields Are Proving Biotech is The Innovation Powerhouse in Healthcare
Biotech is the best source of innovation in R&D, making its companies the darlings of pharma. Which therapeutic fields belong…
