• Latest Posts

European Commission approves first gene therapy for hemophilia B

Peter MacCallum Cancer Centre and Cartherics to work on CAR-T cell therapy for ovarian cancer

GC Biopharma acquiring hemophilia rare disease pipeline

Opinion 28 Feb 2023

Life changing treatments for rare disease – a beacon of hope

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5 advancements in rare disease research over the past year

10 biotech companies making a difference in rare diseases

Resalis Therapeutics receives €10M to develop obesity and NAFLD treatment

Beyond Biotech podcast 35: Rare Disease Day

AELIX announces ‘important step towards HIV eradication’

Sanofi hemophilia drug gets FDA approval

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