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Best in Biotech 22 Aug 2024

Seven companies transforming the biotech industry in Italy

…The company is leveraging these AAV vectors to target specific mutations that cause retinal diseases and correct defective genes responsible for the diseases to halt or even reverse the progression…

August 22, 2024 - 9 minutesmins - By Jules Adam

Best in Biotech 17 Jun 2025

Six kidney disease companies you should know about in 2025

…delivered to the kidney, which has historically been a challenging organ to access for genetic medicines, for the treatment of systemic diseases and renal diseases. It does this with the…

June 17, 2025 - 9 minutesmins - By Willow Shah-Neville

Best in Biotech 8 May 2019

Top 10 Biotechs in Lausanne

…diagnostics Sophia Genetics applies AI to the analysis of the human genome with the goal of making personalized treatment recommendations to patients with cancer or genetic diseases. The company has…

May 8, 2019 - 7 minutesmins - By David Cox

Miquel Vila Perelló gene therapy SpliceBio

Interview 28 Nov 2022

Breaking barriers to gene therapies for childhood rare diseases

The majority of known rare genetic diseases affect children, and gene therapies could help them live normal lives. Miquel Vila-Perelló, CEO and co-founder of the Spanish biotech SpliceBio, outlines how…

November 28, 2022 - 5 minutesmins - By Jonathan Smith

In Depth 9 Dec 2024

CAR-T cell therapy for lupus: An emerging field with great potential

…white blood cell that makes infection-fighting proteins called antibodies. CAR-T researchers are currently very focused on a group of autoimmune diseases referred to as B-cell-mediated diseases, which includes lupus. In…

December 9, 2024 - 10 minutesmins - By Willow Shah-Neville

News and Trends 16 Oct 2019

UK Firm Raises €51M to Repurpose Drugs for Rare Diseases Using AI

…AI to collect extensive medical research data about rare diseases and existing drugs. The AI uses these data to predict which drugs could treat incurable rare diseases such as fragile…

October 16, 2019 - 2 minutesmins - By Jonathan Smith

News and Trends 16 Mar 2023

Inspire Biotherapeutics launches to target lung diseases through gene therapy

…platform can be applied to treat many lung diseases. These include interstitial lung disease, pulmonary fibrosis, other monogenic lung diseases and cystic fibrosis. Inspire Biotherapeutics’ scientific founders – Bernard Thébaud,…

March 16, 2023 - 2 minutesmins - By Jim Cornall

Centogene Rare Disease Diagnostics Series A

News and Trends 13 Jun 2017

German Biotech Raises €25M to Fuel Diagnostics of Rare Diseases

Centogene has raised €25M in a Series A round to support the global expansion of its genome analysis platform, which is specialized in rare diseases. The German biotech Centogene is…

June 13, 2017 - 2 minutesmins - By Melanie De Almeida

In Depth 31 Jan 2017

Biologicals on the Brain: Biotech in Neurodegenerative Disease

…particularly focused on rare diseases with a significant CNS component. We feel that our technology platform can be leveraged across a substantial number of these rare diseases that affect the…

January 31, 2017 - 7 minutesmins - By Diana Kwon

Vaccines for difficult-to-treat diseases

Best in Biotech 12 Apr 2023

6 new vaccines being developed for difficult-to-treat diseases

…are able to prevent more than 20 life-threatening diseases, in turn preventing 3.5 to five million deaths every year from diseases such as diphtheria, tetanus, influenza and measles. Vaccines are…

April 12, 2023 - 10 minutesmins - By Willow Shah-Neville

News and Trends 28 Feb 2017

It’s Global Rare Disease Day! What Cures is Biotech Cooking Up?

…faced by patients with a rare disease. In the EU alone, rare diseases affect 30 million citizens, and there are over 6,000 rare diseases that affect from dozens to thousands…

February 28, 2017 - 5 minutesmins - By Clara Rodríguez Fernández

Best in Biotech 1 Jun 2023

Five ophthalmology biotech companies to look out for

There are hundreds of different eye diseases, with some of the most common major eye diseases including age-related macular degeneration (AMD) – an age-related eye disease that can blur central…

June 1, 2023 - 6 minutesmins - By Willow Shah-Neville

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Search Results for: metabolic diseases

Seven companies transforming the biotech industry in Italy

Six kidney disease companies you should know about in 2025

Top 10 Biotechs in Lausanne

Breaking barriers to gene therapies for childhood rare diseases

CAR-T cell therapy for lupus: An emerging field with great potential

UK Firm Raises €51M to Repurpose Drugs for Rare Diseases Using AI

Inspire Biotherapeutics launches to target lung diseases through gene therapy

German Biotech Raises €25M to Fuel Diagnostics of Rare Diseases

Biologicals on the Brain: Biotech in Neurodegenerative Disease

6 new vaccines being developed for difficult-to-treat diseases

It’s Global Rare Disease Day! What Cures is Biotech Cooking Up?

Five ophthalmology biotech companies to look out for

Subscribe to our newsletter to get the latest biotech news!

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

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