You searched for metabolic diseases - Page 52 of 62

gene therapy ada scid orchard therapeutics

News and Trends 25 Feb 2019

Orchard Achieves Good Survival with Cell Therapy for Rare Immune Deficiency

…up to the task. Other diseases in its hit list include rare diseases such as the metabolic disease Sanfilippo type A and the blood condition transfusion-dependent beta-thalassemia. Images from Shutterstock…

February 25, 2019 - 2 minutesmins - By Jonathan Smith

News and Trends 27 Jun 2022

Trial for adults with late onset Pompe disease halted due to serious adverse event

…therapies. The company says it strives to identify, develop and deliver therapies for patients with genetic diseases who currently have few or no effective treatment options. Astellas is reviewing the…

June 27, 2022 - 3 minutesmins - By Liza Laws

News and Trends 27 Aug 2024

Could microbiome drugs be the key to unlocking checkpoint inhibitors’ potential?

…and our metabolic system, and there is an increasing appreciation of the importance of the gut-brain axis.” Research has also been focused on more precise benefits of microbiome modulation. “In…

August 27, 2024 - 11 minutesmins - By Jules Adam

News and Trends 12 Jan 2018

This Collaboration Will Develop a New Epilepsy Gene Therapy for In-Need Patients

…a neurotransmitter, which acts on NPY receptors to trigger a number of central and peripheral effects on the endocrine and metabolic systems, as well as various regulatory functions. Epilepsy is…

January 12, 2018 - 2 minutesmins - By Alex Dale

nash northsea therapeutics, liver disease, disease modeling

News and Trends 8 Jan 2020

NorthSea Therapeutics Raises €36M to Complete NASH Phase II Trial

…simultaneously target diverse metabolic and inflammatory pathways in distinct cell populations is a unique attribute of SEFAs, making them highly suited to the treatment of NASH and fibrosis,” said de…

January 8, 2020 - 2 minutesmins - By Jonathan Smith

In Depth 8 Oct 2024

Top biotech deals of September 2024

…It partnered with Swiss precision medicines company HAYA Therapeutics to employ HAYA’s RNA platform to hunt for drugs that can treat obesity and related metabolic conditions. HAYA is eligible to…

October 8, 2024 - 6 minutesmins - By Roohi Mariam Peter

circulating tumor cells, cancer, clinical trials

News and Trends 28 Jul 2022

Kelun-Biotech announces joint license agreement with MSD for drug targeting solid tumors

…therapeutics as well as small molecule discovery and development. The company’s current pipeline includes 55 therapeutic programs for the treatment of cancers, autoimmune conditions, infectious diseases, and metabolic syndromes. development….

July 28, 2022 - 3 minutesmins - By Liza Laws

News and Trends 22 Jan 2018

No More Mosquito Bites? Targeting These Genes Could Prevent Future Outbreaks!

Researchers may have found a way to stop the female mosquitoes from biting you, which could help to prevent the spread of diseases like malaria. Scientists at the University of…

January 22, 2018 - 3 minutesmins - By Alex Dale

News and Trends 15 Jun 2023

New data on breath biopsy for early detection of lung cancer

…cancer’ describes a complementary EVOC probe approach for the early detection of lung cancer based on aldo-keto reductase (AKR) activity, a metabolic process linked with the body’s reaction to the…

June 15, 2023 - 3 minutesmins - By Jim Cornall

Best in Biotech 25 Apr 2024

8 of the most expensive drugs in biopharma: Unraveling the costliest medications

…in 2023 compared to the previous year, reflecting in part the industry’s embrace of expensive therapies for rare diseases like muscular dystrophy. Gene therapies in particular have emerged as some…

April 25, 2024 - 12 minutesmins - By Willow Shah-Neville

In Depth 6 Feb 2023

The biggest private biotech investments in January 2023

…help of biomaterials. Meanwhile, the U.S.-Chinese firm Structure Therapeutics went public on the Nasdaq raising $161.1 million to fund the development of oral treatments for chronic metabolic and pulmonary diseases….

February 6, 2023 - 4 minutesmins - By Jonathan Smith

News and Trends 9 Jun 2023

Med-Life Discoveries to start rare pediatric disease trial

…lead compound PPI-1011. This is a milestone on the path towards a potential therapy for children with RCDP. Med-Life Discoveries’ focus is the development of plasmalogen therapeutics for complex diseases…

June 9, 2023 - 4 minutesmins - By Jim Cornall

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Search Results for: metabolic diseases

Orchard Achieves Good Survival with Cell Therapy for Rare Immune Deficiency

Trial for adults with late onset Pompe disease halted due to serious adverse event

Could microbiome drugs be the key to unlocking checkpoint inhibitors’ potential?

This Collaboration Will Develop a New Epilepsy Gene Therapy for In-Need Patients

NorthSea Therapeutics Raises €36M to Complete NASH Phase II Trial

Top biotech deals of September 2024

Kelun-Biotech announces joint license agreement with MSD for drug targeting solid tumors

No More Mosquito Bites? Targeting These Genes Could Prevent Future Outbreaks!

New data on breath biopsy for early detection of lung cancer

8 of the most expensive drugs in biopharma: Unraveling the costliest medications

The biggest private biotech investments in January 2023

Med-Life Discoveries to start rare pediatric disease trial

Subscribe to our newsletter to get the latest biotech news!

10 oncology deals in 2025 spotlight where industry leaders are betting big

10 biotech companies leading the way in Denmark

Webinar: Advancements in antimalarial drug discovery and development

Six psychedelic drug companies aiming to revolutionize mental health treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

10 oncology deals in 2025 spotlight where industry leaders are betting big

10 biotech companies leading the way in Denmark

Webinar: Advancements in antimalarial drug discovery and development

Six psychedelic drug companies aiming to revolutionize mental health treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

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