Tag
Tag: Rare disease
Update: Novartis’ Gene Therapy Zolgensma Gets Nod from EU
Phase III Failure Sinks Drug for Rare Neurological Disorder
Update: FDA Imposes No Penalties for Novartis Data Manipulation Scandal
Ipsen Resumes Phase III Testing for Rare Disease Drug and Abandons Pediatric Trial
How Can We Improve the Diagnosis and Treatment of Rare Diseases?
First-in-Class Drug For Inherited Metabolic Diseases Funded with €25M
Harnessing Genetic Suppression to Treat Rare Disease
Rare Inflammatory Disease Drug Beats Immunosuppressants in Phase III
Mereo BioPharma’s Brittle Bone Disease Drug Stumbles in Phase II
€51M Nasdaq IPO Will Fund Centogene’s Rare Disease Diagnostics
