Gene therapy approval “game changer” in hemophilia B treatment
The approval of CSL's gene therapy Hemgenix has ushered in a new era for hemophilia…
As one of the biggest success stories of the 21st century, gene therapy is providing hope for treating diseases that once seemed incurable. Any genetic mutation causing disease could theoretically be fixed by inserting a new copy of the faulty gene. This means that gene therapy has the potential to treat some previously incurable conditions with a single dose.
By 2025, the FDA expects to approve between 10 and 20 gene therapies each year, and we are already seeing an increase in the number of approvals today. However, the field continues to face a number of obstacles ranging from safety concerns to manufacturing shortages. Read on to get the latest in the gene therapy field.
Gene Therapy Industry Report 2021
In this report, we take a closer look at the growing gene therapy market, current development and manufacturing challenges, and the exciting future ahead for this industry.
Go to ReportThe approval of CSL's gene therapy Hemgenix has ushered in a new era for hemophilia…
Slovenian-based Sartorius BIA Separations (BIA), a bio-chromatography company, and Australia's Exopharm Ltd., a company working…
CSL has revealed that the U.S. Food and Drug Administration (FDA) has approved HEMGENIX (etranacogene…
Replay has announced the launch of Telaria, a herpes simplex virus (HSV) gene therapy company…
The Cell and Gene Therapy Catapult (CGT Catapult) has published its ninth annual U.K. cell…
By 2026, pharma industry insiders anticipate cell and gene therapy sales to significantly increase, with…
Sensorion has announced that the US Food and Drug Administration (FDA) has granted rare pediatric…
Gene editing has come far in the past decade. However, the field is still finding…
Gene delivery technology company VectorBuilder Inc. has announced the completion of $57 million in funding.…
Replay Bio has announced the launch of Eudora, an HSV (herpes simplex virus) gene therapy…
French companies ABL and RD-Biotech have signed a strategic partnership to cover cell and gene…
Healthcare company Syncona Limited says its newly established portfolio company has agreed to acquire, by…