News and Trends 4 Apr 2023
New research may lead to gene therapies for kidney disease
Autosomal dominant polycystic kidney disease (ADPKD) is the most common potentially lethal genetic disease—about a half million people in the…
Gene therapy
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News and Trends 30 Mar 2023
Could new riboswitch make gene therapy safer?
Turning genes on and off as easily and predictably as flicking a switch could be a powerful tool in medicine…
News and Trends 16 Mar 2023
Inspire Biotherapeutics launches to target lung diseases through gene therapy
Inspire Biotherapeutics Inc., an emerging Canadian biotech company with a mission to create gene therapies for monogenic and acquired diseases…
News and Trends 15 Mar 2023
Nanite receives funding to deliver genetic therapies to the lungs
Nanite Inc. has announced an investment from the Cystic Fibrosis Foundation of up to $2 million to develop gene delivery…
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Interview 8 Mar 2023
Phacilitate’s Women in Advanced Therapies program supports women in science
Marlin Frechette is the chief quality and compliance officer at FUJIFILM Irvine Scientific. But she has another role. Frechette is…
News and Trends 3 Mar 2023
Beyond Biotech podcast 36: Bio-Europe Spring and Cellular Origins
Two of the interviews on the podcast today are related to Bio-Europe Spring. There are conversations with Rosie Bernard, senior…
Interview 3 Mar 2023
Interview: how has the first gene therapy for hemophilia B transformed research?
Hemophilia B, a rare disease that affects more than 230,000 people worldwide is caused by the lack of or defective…
News and Trends 3 Mar 2023
Porton and DanausGT look to boost development of gene and cell therapy
Porton Advanced Solutions Ltd. and DanausGT Biotechnology Co., Ltd. have announced a strategic collaboration in gene and cell therapy pipelines…
News and Trends 2 Mar 2023
New lipid nanoparticle CRISPR delivery system developed
Lipid nanoparticles have been used to encapsulate CRISPR-Cas9 and deliver it to cells in mice, where it was highly effective…
News and Trends 28 Feb 2023
European Commission approves first gene therapy for hemophilia B
The European Commission has approved the first gene therapy for the treatment of hemophilia B developed by biotech company CSL…
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Opinion 28 Feb 2023
Life changing treatments for rare disease – a beacon of hope
By Sander Slootweg, managing partner, Forbion More than 300 million people around the globe are affected by a rare disease.…
News and Trends 17 Feb 2023
Report: China leads the way with phase 1 studies
Novotech, an Asia Pacific biotech CRO, has published a new global report on phase 1 trial activity including current metrics…
News and Trends 10 Feb 2023
Rocket Pharmaceuticals receives FDA RMAT designation for Danon disease gene therapy treatment
Rocket Pharmaceuticals, Inc says the U.S. Food and Drug Administration (FDA) has granted regenerative medicine advanced therapy (RMAT) designation to…
News and Trends 9 Feb 2023
Cell and Gene Therapy Catapult boost for life science campus
The Cell and Gene Therapy Catapult (CGT Catapult), an independent U.K. innovation and technology organization specializing in the advancement of…
News and Trends 31 Jan 2023
Sensorion and EVEON collaborating on injection system to deliver gene therapy inner ear treatments
Sensorion and EVEON are collaborating on the design and development of an injection system for the delivery of Sensorion’s gen…
News and Trends 24 Jan 2023
Funding for university to develop new motor neuron disease therapies
Medical research charity LifeArc, the Motor Neurone Disease Association (MND Association) and the My Name’5 Doddie Foundation have jointly awarded…
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In Depth 17 Jan 2023
Cell and gene therapies gain momentum in Basel
Companies specializing in the research and development of innovative cell and gene therapies continue to spring up all around the…
News and Trends 17 Jan 2023
TTP spinout Cellular Origins to focus on cell and gene therapies
TTP plc, a technology and product development company, has announced the launch of Cellular Origins. Cellular Origins is a TTP…
Sponsored by WuXi Advanced Therapies
17 Jan 2023Navigating cell and gene therapy manufacturing with a long-term partnership
Cell and gene therapies have proven to be promising treatments for cancers and genetic diseases, but developers face key challenges…
News and Trends 12 Jan 2023
Team wins $149M contract for National Institute of Neurological Disorders and Stroke
A team consisting of Battelle, AmplifyBio and Andelyn Biosciences has won a seat on an eight-year, $149 million indefinite delivery,…
