Gene therapy Archives

gene therapy cardiac rare disease biomarin dinaqor

News and Trends 7 May 2020

BioMarin Partners Swiss Biotech to Develop Cardiac Gene Therapies

US biotech BioMarin has partnered Swiss startup DiNAQOR to develop gene therapies to treat rare, inherited cardiac diseases. DiNAQOR will initially receive an upfront payment from BioMarin, followed by developmental, regulatory, and commercial milestone payments and a percentage of royalties on later sales. No financial details of the collaboration were revealed by either company. “We […]

May 7, 2020 - 2 minutesmins - By Helen Albert

Altheia Science gene therapy autoimmune disease

News and Trends 8 Apr 2020

Evotec Makes Move into Gene Therapy with Takeda Deal

German biotech giant Evotec has moved into gene therapy and partnered with Takeda to develop new therapies in oncology, rare diseases, neuroscience, and gastroenterology. The two companies did not reveal financial details of the collaboration, but did say that it will be a multi-year alliance that adds to Evotec’s existing deal with the big pharma […]

April 8, 2020 - 3 minutesmins - By Helen Albert

novartis avexis zolgensma fda data manipulation

News and Trends 2 Apr 2020

Update: FDA Imposes No Penalties for Novartis Data Manipulation Scandal

Update (02/04/2020): The FDA has concluded an investigation into a data manipulation scandal surrounding the approval of Novartis’ gene therapy Zolgensma, and has decided against sanctions. The FDA launched an investigation into the manipulated data surrounding the gene therapy application last year, and recently reported that the investigated data violations didn’t meet the threshold for […]

April 2, 2020 - 3 minutesmins - By Jonathan Smith

london ori biotech cell therapy manufacturing

Startup Scout 28 Feb 2020

This Startup Is Automating the Manufacture of Gene and Cell Therapies

In London, the firm Ori Biotech is developing an automated way to manufacture gene and cell therapies, a bottleneck for many biotech companies. Mission: To develop a robotic system to automate the labor-intensive tasks involved in manufacturing cell and gene therapies, such as gene transduction and cell expansion. Gene and cell therapies are maturing as […]

February 28, 2020 - 3 minutesmins - By Jonathan Smith

News and Trends 19 Feb 2020

Belgian Biotech Raises €50M to Make Gene Therapy Manufacturing Cheaper

An equity investment worth up to €50M will push to market Univercells’ manufacturing technology, which is designed to reduce the costs of viral vector production for gene therapies. The investment comes from Gamma Biosciences, an investment platform supported by the US investor KKR. Gamma Biosciences aims to acquire and invest in businesses developing gene and […]

February 19, 2020 - 2 minutesmins - By Jonathan Smith

stilla technologies pcr molecular diagnostics

News and Trends 11 Feb 2020

French Biotech Raises €20M to Make Precision Molecular Diagnostics

Stilla Technologies has raised a €20M Series C round to fund its mission to produce next-generation microchips that make molecular diagnostics more precise and user-friendly than currently available lab technology. Contributors to the round included Stilla’s existing investors, such as Illumina Ventures, Kurma Partners and Idinvest Partners. Stilla also added the Chinese company TUS-Holdings to […]

February 11, 2020 - 2 minutesmins - By Jonathan Smith

News and Trends 28 Jan 2020

A Future Gene Therapy Could Be Delivered in Tiny ‘Nanocontainers’

A Swiss research group has developed tiny plastic particles that could carry gene therapies to the center of the cell with less risk of getting attacked by the immune system than conventional gene therapies. The majority of gene therapies in use today are delivered to the DNA of target cells using viral vectors. While efficient […]

January 28, 2020 - 3 minutesmins - By Jonathan Smith

News and Trends 18 Jan 2020

DNA Data Storage Project Receives €20.7M from US Intelligence Agency

A DNA data storage project, involving French biotech DNA Script, has been awarded a contract worth up to €20.7M from the US Intelligence Advanced Research Projects Activity agency to develop a prototype instrument able to store and retrieve 1 terabyte of information in 24 hours. The Molecular Encoding Consortium, led by Robert Nicol at the Broad […]

January 18, 2020 - 3 minutesmins - By External Contributor

News and Trends 14 Jan 2020

Bluebird Bio Launches First Gene Therapy for Beta Thalassemia in Germany

The US company bluebird bio has launched the first gene therapy for the blood disorder transfusion-dependent beta thalassemia in the EU, with a hospital in Germany becoming its first qualified treatment center. Bluebird bio’s gene therapy, branded as Zynteglo, was given conditional market approval by the EU in June 2019. It was the first gene […]

January 14, 2020 - 3 minutesmins - By Jonathan Smith

News and Trends 10 Jan 2020

Eyevensys’ Gene Therapy for Blindness Boosted with €27M Series B

The French company Eyevensys has raised €27M to fund the launch of a phase II trial for its lead candidate, a non-viral gene therapy for an eye condition called uveitis that can lead to blindness. The Series B round was led by the Boehringer Ingelheim Venture Fund. New investors to Eyevensys in this round included […]

January 10, 2020 - 3 minutesmins - By Jonathan Smith

Best in Biotech 30 Dec 2019

European Biotech’s Top News in 2019

With the year coming to a close, it’s time to review the most important biotech news events that took place in the European biotech industry in 2019. It has been a solid year for the European biotech industry. In 2019, venture capital funding in Europe continued to be high after a very good year in […]

December 30, 2019 - 10 minutesmins - By Jonathan Smith

News and Trends 20 Dec 2019

Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost

The UK gene therapy biotech Freeline Therapeutics is to receive an investment worth €72M (£61.1M) from the UK VC firm Syncona in a Series C round to fund the clinical development of gene therapies for the blood disorder hemophilia B, Fabry disease, and other rare conditions. Of the €72M commitment, Syncona has already wired €36M […]

December 20, 2019 - 2 minutesmins - By Jonathan Smith

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Gene therapy

BioMarin Partners Swiss Biotech to Develop Cardiac Gene Therapies

Evotec Makes Move into Gene Therapy with Takeda Deal

Update: FDA Imposes No Penalties for Novartis Data Manipulation Scandal

This Startup Is Automating the Manufacture of Gene and Cell Therapies

Belgian Biotech Raises €50M to Make Gene Therapy Manufacturing Cheaper

French Biotech Raises €20M to Make Precision Molecular Diagnostics

A Future Gene Therapy Could Be Delivered in Tiny ‘Nanocontainers’

DNA Data Storage Project Receives €20.7M from US Intelligence Agency

Bluebird Bio Launches First Gene Therapy for Beta Thalassemia in Germany

Eyevensys’ Gene Therapy for Blindness Boosted with €27M Series B

European Biotech’s Top News in 2019

Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost

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The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

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Advertise with us

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

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