Gene therapy Archives

News and Trends 14 Jan 2020

Bluebird Bio Launches First Gene Therapy for Beta Thalassemia in Germany

The US company bluebird bio has launched the first gene therapy for the blood disorder transfusion-dependent beta thalassemia in the EU, with a hospital in Germany becoming its first qualified treatment center. Bluebird bio’s gene therapy, branded as Zynteglo, was given conditional market approval by the EU in June 2019. It was the first gene […]

January 14, 2020 - 3 minutesmins - By Jonathan Smith

News and Trends 10 Jan 2020

Eyevensys’ Gene Therapy for Blindness Boosted with €27M Series B

The French company Eyevensys has raised €27M to fund the launch of a phase II trial for its lead candidate, a non-viral gene therapy for an eye condition called uveitis that can lead to blindness. The Series B round was led by the Boehringer Ingelheim Venture Fund. New investors to Eyevensys in this round included […]

January 10, 2020 - 3 minutesmins - By Jonathan Smith

Best in Biotech 30 Dec 2019

European Biotech’s Top News in 2019

With the year coming to a close, it’s time to review the most important biotech news events that took place in the European biotech industry in 2019. It has been a solid year for the European biotech industry. In 2019, venture capital funding in Europe continued to be high after a very good year in […]

December 30, 2019 - 10 minutesmins - By Jonathan Smith

News and Trends 20 Dec 2019

Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost

The UK gene therapy biotech Freeline Therapeutics is to receive an investment worth €72M (£61.1M) from the UK VC firm Syncona in a Series C round to fund the clinical development of gene therapies for the blood disorder hemophilia B, Fabry disease, and other rare conditions. Of the €72M commitment, Syncona has already wired €36M […]

December 20, 2019 - 2 minutesmins - By Jonathan Smith

dna data storage self replicating machine

News and Trends 9 Dec 2019

Scientists Use DNA Data Storage to Hide Information in Everyday Objects

Scientists have developed a method for storing DNA data in 3D-printed objects, which could one day allow machines to replicate themselves. The group, based at ETH Zurich, Switzerland, as well as in Israel and the US, began by synthesizing DNA molecules that encode blueprints of the Stanford bunny, a rabbit-shaped object commonly used in testing […]

December 9, 2019 - 4 minutesmins - By Jonathan Smith

vigeneron germany gene therapy adenoviral vector

More News! 28 Nov 2019

German Biotech to Develop Next-Generation Gene Therapy for Blindness

The German biotech ViGeneron has raised an undisclosed sum in a Series A round to fund the development of an ophthalmic gene therapy that could deliver bigger DNA sequences into a wider range of cells than current technology. The round was led by two Chinese investors, the VC firm Sequoia Capital China and the pharma […]

November 28, 2019 - 2 minutesmins - By Jonathan Smith

EU regulations cell gene therapy clinical trials

News and Trends 5 Nov 2019

EU Regulations Are Holding Back Gene and Cell Therapy Clinical Trials

European regulations might be responsible for lower numbers of advanced therapy clinical trials running in the region when compared to the US and Asia. Europe has historically been a pioneer in advanced therapies, such as cell and gene therapy. Europe was the first region to approve a gene therapy, and it boasts the highest number […]

November 5, 2019 - 4 minutesmins - By Clara Rodríguez Fernández

spinal muscular atrophy zolgensma novartis gene therapy

News and Trends 30 Oct 2019

Trial Testing Spinal Application of Zolgensma Put on Hold by FDA

The FDA has placed a partial hold on clinical trials testing a new application method for Zolgensma, Novartis’ gene therapy for the genetic disease spinal muscular atrophy, after it showed the potential to cause serious side effects in animal models. Spinal muscular atrophy is a life-threatening condition that usually arises when the patient is between […]

October 30, 2019 - 2 minutesmins - By Jonathan Smith

More News! 28 Oct 2019

UK Company Synthesizes Long DNA Molecules with 85% Accuracy

The UK biotech Camena Bioscience has proven it can synthesize long DNA molecules with more accuracy than traditional chemical synthesis. Camena tested its technology’s ability to accurately synthesize DNA molecules with a length of 300 nucleotides — the building blocks of DNA. Using Camena’s technology, 85% of the synthesized DNA molecules were accurate to the […]

October 28, 2019 - 2 minutesmins - By Jonathan Smith

gene therapy cell therapy advanced therapy 4BIO

News and Trends 9 Sep 2019

4BIO Capital Raises €45M Fund to Invest in Advanced Therapies

The London-based life sciences investor 4BIO Capital has raised €45M in the first close of a fund to nurture companies developing advanced therapies such as gene and cell therapies. This is the first closing of 4BIO’s second fund, called 4BIO Ventures II, which is expected to total €136M ($150M) by late 2020. The fund will […]

September 9, 2019 - 3 minutesmins - By Jonathan Smith

News and Trends 5 Sep 2019

Orchard’s Gene Therapy Improves Children’s Motor Ability

Orchard Therapeutics’ gene therapy for metachromatic leukodystrophy (MLD) resulted in motor ability improvements more than six times over the target endpoint, according to data released at a recent symposium. “Metachromatic leukodystrophy is a rare disease that affects the brain,” explained Mark Rothera, CEO of Orchard Therapeutics. “Kids born with MLD lose motor function very fast […]

September 5, 2019 - 3 minutesmins - By Clara Rodríguez Fernández

News and Trends 3 Sep 2019

Gyroscope Targets Age-Related Blindness with €55M Series B

UK gene therapy biotech Gyroscope Therapeutics has secured €55.4M in Series B funding to target age-related macular degeneration. Life sciences investor Syncona, which is backed by the UK’s Wellcome Trust, continued its support of the company contributing €52.7M to the round. This brings its total investment in Gyroscope to €90M since the biotech was founded […]

September 3, 2019 - 2 minutesmins - By Helen Albert

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Gene therapy

Bluebird Bio Launches First Gene Therapy for Beta Thalassemia in Germany

Eyevensys’ Gene Therapy for Blindness Boosted with €27M Series B

European Biotech’s Top News in 2019

Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost

Scientists Use DNA Data Storage to Hide Information in Everyday Objects

German Biotech to Develop Next-Generation Gene Therapy for Blindness

EU Regulations Are Holding Back Gene and Cell Therapy Clinical Trials

Trial Testing Spinal Application of Zolgensma Put on Hold by FDA

UK Company Synthesizes Long DNA Molecules with 85% Accuracy

4BIO Capital Raises €45M Fund to Invest in Advanced Therapies

Orchard’s Gene Therapy Improves Children’s Motor Ability

Gyroscope Targets Age-Related Blindness with €55M Series B

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Illuminating biotech in the City of Light: Inside Paris’s thriving ecosystem

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New report: Artificial intelligence and the future of antibody discovery

Stem cell therapy: a potential cure for hearing loss?

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

Illuminating biotech in the City of Light: Inside Paris’s thriving ecosystem

ASCO 2025: key highlights in cancer therapeutics

New report: Artificial intelligence and the future of antibody discovery

Stem cell therapy: a potential cure for hearing loss?

Connect with decision-makers and researchers worldwide for collaborative opportunities

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