Gene therapy Archives

News and Trends 29 Jul 2016

Gene Therapy for severe Hemophilia has new Phase I/II Results

uniQure has new data from the Phase I/II trial of its gene therapy for Hemophilia B, a rare genetic disorder. After 9 months, the therapy maintains 75% reduction of transfusions. A good sign for the therapy’s durability. Although quite rare (1 in 20,000 male births), Hemophilia B is famous for being spread in European royal […]

July 29, 2016 - 3 minutesmins - By Denise Neves Gameiro

News and Trends 21 Jul 2016

UPDATED: French Gene Therapy for Blindness Launches another IPO

Update (21/07/2016): Gensight has successfully completed its IPO, raising €40M. This brings the Biotech’s total market capitalization to near €149M. The option of round oversubscription to €46M is still open. Originally published on 5/7/2016 After canceling its NASDAQ IPO back in April, GenSight is now launching on the Euronext Paris. It wants to raise €40M in total, […]

July 21, 2016 - 2 minutesmins - By Denise Neves Gameiro

News and Trends 8 Jul 2016

French Startup raised €4M for Gene Therapy to fix specific Types of Blindness

Horama is developing gene therapies for several hereditary retinal dystrophies. It has now raised €4M in its Series A round, which will speed up development of two candidates. Eye disorders are a popular indication for gene therapies, especially after the first gene therapy approvals – uniQure’s Glybera and GSK’s Strimvelis. Some other players in ophthalmologic […]

July 8, 2016 - 2 minutesmins - By Denise Neves Gameiro

News and Trends 28 Jun 2016

Will the Leading Italian Biotech soon have its First Cell therapy on the Market?

MolMed has received conditional market approval for Zalmoxis, an ex vivo genetically engineered cell therapy that stops immune rejection of transplanted hematopoietic stem cells. This is a big step forward in a key treatment for blood cancers. A transplant of hematopoietic stem cells (cells that give origin to blood cells) is often used as part of treatments for […]

June 28, 2016 - 2 minutesmins - By Denise Neves Gameiro

News and Trends 7 Jun 2016

German Biotech partners up in the US for scalable viral vector production in Gene Therapy

Cevec is joining forces with US-based Paragon. The objective is to make Cevec’s scalable CAP expression technology the industry standard for glycoproteins and viral vectors in gene therapies. Based in Cologne (Germany), Cevec tackles with its human cell-based expression systems (CAP-GT and CAP-Go) two big challenges in Biotech manufacturing – industrial scale production of viral vectors […]

June 7, 2016 - 4 minutesmins - By Denise Neves Gameiro

News and Trends 6 May 2016

This Dutch Gene Therapy is on the shelf and seems to Work. But nobody is buying…

uniQure‘s Glybera was approved in Europe in 2012, making it the first gene therapy on the market in the West. But so far this €1M therapy has only been bought once… The approval of Glybera was an important milestone for Biotech. After years of being deemed too risky (after the death of Jesse Gelsinger in 1999), a […]

May 6, 2016 - 3 minutesmins - By Denise Neves Gameiro

News and Trends 6 May 2016

Stem cell Biotech gets €26M to Start-off Gene Therapy Development for Children

Orchard Therapeutics has just been launched with a €26M investment led by a major investor. It will be developing gene therapies for a range of blood-related disorders in children. Based in London, Orchard Therapeutics may have just been founded, but it’s based on a long scientific track record. Its founding scientists have been pioneering the area […]

May 6, 2016 - 3 minutesmins - By Denise Neves Gameiro

News and Trends 26 Apr 2016

Illumina is Suing over NGS Prenatal Screening… Again

Genoma is being sued by Illumina over four patents covering technology for prenatal testing, that uses NGS to diagnose fetal defects. After suing Oxford Nanopore over porin technology, Illumina is back to another contentious field – their patents for a type of non-invasive prenatal testing (NIPT). Illumina has filed a patent infringement suit in the Federal […]

April 26, 2016 - 2 minutesmins - By Denise Neves Gameiro

News and Trends 11 Apr 2016

Modern Biotechnology is Now 40 – Happy Birthday!

Genentech has turned 40 years old this month – quite a milestone for the pioneer of modern biotechnology, which is still rocking it in San Francisco, US. It all began with an experiment conducted by a team led by Herbert Boyer of the University of California San Francisco (UCSF), studying antibiotic resistance plasmids in E. […]

April 11, 2016 - 3 minutesmins - By Denise Neves Gameiro

News and Trends 5 Apr 2016

How can we Optimise DNA Extraction from Human Blood for more Sensitive NGS Analysis?

The increasing relevance of Next Generation Sequencing (NGS) in genetic research means there is a high demand for nucleic acid isolation from human fluids. So how can we perform efficient DNA extraction from human blood? NGS has revolutionised genetic research, by serving as a powerful processing technology, cutting time taken to run genetic analysis and also the cost. […]

April 5, 2016 - 3 minutesmins - By Dani Bancroft

News and Trends 17 Mar 2016

GSK partners to Scale Manufacturing of CAR-T Therapies

Production of CAR-T therapies seems to be one of the biggest challenge of this promising technology. Miltenyi Biotec (Germany) and GSK have entered a new partnership to combine the clinical development of cell and gene therapies with manufacturing expertise. Milteniy is a German company of 1600 employees developing products for biomedical research and cellular therapy. It’s not the first […]

March 17, 2016 - 3 minutesmins - By Denise Neves Gameiro

News and Trends 11 Mar 2016

Biotech of the Week: Mission Therapeutics and a Cambridge Pathway against Cancer

From East to West, this week we say goodbye to Hungary and head up towards Queen Elizabeth II’s United Kingdom. Cambridge, known for its World renowned Academia is where Mission Therapeutics, our Biotech of the Week is located. City: Cambridge (UK) Founded: 2011 Employees: 30 Total raised: €110M (as of 02/2016) CEO: Anker Lundemose Mission: Founded in 2011, Mission Therapeutics, […]

March 11, 2016 - 1 minutemin - By Joachim Eeckhout

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Gene therapy

Gene Therapy for severe Hemophilia has new Phase I/II Results

UPDATED: French Gene Therapy for Blindness Launches another IPO

French Startup raised €4M for Gene Therapy to fix specific Types of Blindness

Will the Leading Italian Biotech soon have its First Cell therapy on the Market?

German Biotech partners up in the US for scalable viral vector production in Gene Therapy

This Dutch Gene Therapy is on the shelf and seems to Work. But nobody is buying…

Stem cell Biotech gets €26M to Start-off Gene Therapy Development for Children

Illumina is Suing over NGS Prenatal Screening… Again

Modern Biotechnology is Now 40 – Happy Birthday!

How can we Optimise DNA Extraction from Human Blood for more Sensitive NGS Analysis?

GSK partners to Scale Manufacturing of CAR-T Therapies

Biotech of the Week: Mission Therapeutics and a Cambridge Pathway against Cancer

Subscribe to our newsletter to get the latest biotech news!

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

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