Interview: how has the first gene therapy for hemophilia B transformed research?
Hemophilia B, a rare disease that affects more than 230,000 people worldwide is caused by…
March 3, 2023 - 8 minutes
Hemophilia
European Commission approves first gene therapy for hemophilia B
The European Commission has approved the first gene therapy for the treatment of hemophilia B…
February 28, 2023 - 3 minutes
GC Biopharma acquiring hemophilia rare disease pipeline
GC Biopharma Corp., a South Korean provider of biopharmaceutical products, has signed an asset purchase…
February 28, 2023 - 2 minutes
Sanofi hemophilia drug gets FDA approval
The U.S. Food and Drug Administration (FDA) has approved Sanofi's ALTUVIIIO [Antihemophilic Factor (Recombinant), Fc-VWF-XTEN…
February 24, 2023 - 4 minutes
CSL closer to gene therapy treatments for hemophilia B patients in Europe
CSL says the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP)…
December 16, 2022 - 2 minutes
Gene therapy approval “game changer” in hemophilia B treatment
The approval of CSL's gene therapy Hemgenix has ushered in a new era for hemophilia…
November 24, 2022 - 7 minutes
FDA approves CSL gene therapy for hemophilia B
CSL has revealed that the U.S. Food and Drug Administration (FDA) has approved HEMGENIX (etranacogene…
November 23, 2022 - 5 minutes
Enzyre secures €12M series A funding to help hemophilia patients test from home
Dutch company, Enzyre, which is developing ambulant diagnostic technology for blood coagulation testing, today (November…
November 2, 2022 - 3 minutes
Beyond Biotech podcast 17: BIO-Europe, National Hemophilia Foundation
This week, we have three interviews. Our guests are: Pam Putz, managing director of EBD…
October 7, 2022 - 2 minutes
Hemophilia drug from Sanofi and Sobi has license application accepted for priority review by FDA
The Biologics License Application (BLA) for Efanesoctocog alfa, a drug to treat the rare and…
August 30, 2022 - 2 minutes
First gene therapy for adults with severe hemophilia approved by EC
The European Commission (EC) has granted conditional marketing authorization for a gene therapy to treat…
August 26, 2022 - 3 minutes
People with hemophilia B could be protected from bleeding by a single dose of a drug currently being trialed
London-based Freeline Therapeutics Holdings plc has just announced that positive data on treating haemophilia has…
July 22, 2022 - 3 minutes
