Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost
The UK gene therapy biotech Freeline Therapeutics is to receive an investment worth €72M (£61.1M)…
20/12/2019 - 2 minutes
Hemophilia
First Potential Gene Therapy for Hemophilia B Restores Blood Clotting in Phase II
A gene therapy developed by the Dutch biotech uniQure increased the activity of a blood…
14/05/2019 - 3 minutes
World’s First Gene Therapy Developer Raises $128M for Hemophilia and Huntington’s
uniQure has raised a substantial public offering on the NASDAQ. The funding could help the Dutch…
03/05/2018 - 2 minutes
Like Finding a Needle in a Haystack: How Are Biotechs Fighting Rare Diseases?
Rare diseases affect fewer than 1 in 2,000 people in Europe and less than 200,000…
28/02/2018 - 8 minutes
How is Biotech Innovating to Treat Hemophilia? Let’s Review
Experts say hemophilia treatment is at a 'precipice of a therapeutic revolution.' From antibodies to…
13/02/2018 - 7 minutes
Interviews, Reviews and Tops: Our Best Biotech Articles from 2017
We love hearing from our readers, and we listen to what they like! Here are…
26/12/2017 - 6 minutes
This Gene Therapy for Hemophilia Can Reduce Bleeding by 70%
UniQure has published clinical data revealing that its gene therapy for hemophilia B is effective…
19/12/2017 - 3 minutes
Smile! Here are the 12 Biggest Biotech Clinical Successes of 2017
Now that we've got the bad news out of the way, we're here to spread…
18/12/2017 - 9 minutes
The Best of the Rest: What Else Happened at this Year’s ASH Conference?
Last weekend marked the 59th Annual Meeting of the American Society of Hematology or ASH.…
11/12/2017 - 4 minutes
Reviewing Gene Therapy: How Close is Biotech to Genetic Cures?
Over 10,000 human diseases are caused by exactly one faulty gene. Gene therapy promises to fix…
28/11/2017 - 8 minutes
Roche’s Potential Hemophilia Blockbuster and Lung Cancer Drug Succeed in the Clinic
Roche has enjoyed a dream start to the week with both its immuno-oncology candidate, Tecentriq,…
20/11/2017 - 2 minutes
Close to Launching Gene Therapy, Dutch Biotech Raises Over $91M on the Nasdaq
Update (2/11/2017): uniQure has closed its public offering raising over $91m (€78M) on the Nasdaq, taking advantage…
02/11/2017 - 3 minutes
