Like Finding a Needle in a Haystack: How Are Biotechs Fighting Rare Diseases?
Rare diseases affect fewer than 1 in 2,000 people in Europe and less than 200,000…
Rare diseases affect fewer than 1 in 2,000 people in Europe and less than 200,000…
Experts say hemophilia treatment is at a 'precipice of a therapeutic revolution.' From antibodies to…
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UniQure has published clinical data revealing that its gene therapy for hemophilia B is effective…
Now that we've got the bad news out of the way, we're here to spread…
Over 10,000 human diseases are caused by exactly one faulty gene. Gene therapy promises to fix…
Update (2/11/2017): uniQure has closed its public offering raising over $91m (€78M) on the Nasdaq, taking advantage…
uniQure is getting ready to start a Phase III clinical trial in 2018 with a…
Bicycle Therapeutics has partnered with Bioverativ to develop a new class of drugs for patients…
Shire has bought exclusive worldwide rights to develop and commercialize a bispecific antibody from Novimmune…
Alnylam and its partner Sanofi are starting a Phase III program to enter its RNAi…
Academic, entrepreneur and now venture partner Trevor Baglin discusses his successful experience working with…