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Beyond Biotech podcast 17: BIO-Europe, National Hemophilia Foundation

Hemophilia drug from Sanofi and Sobi has license application accepted for priority review by FDA

First gene therapy for adults with severe hemophilia approved by EC

People with hemophilia B could be protected from bleeding by a single dose of a drug currently being trialed

Study results reveal bleeding episodes are significantly reduced by hemophilia drug

Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost


First Potential Gene Therapy for Hemophilia B Restores Blood Clotting in Phase II

World’s First Gene Therapy Developer Raises $128M for Hemophilia and Huntington’s

Like Finding a Needle in a Haystack: How Are Biotechs Fighting Rare Diseases?

This Gene Therapy for Hemophilia Can Reduce Bleeding by 70%