On the podcast this week, we are looking at recent advances in treating certain liver diseases. Jennifer Schranz is senior vice president and global head of rare diseases in the…
Spanish researchers have developed a way to diagnose neurodegenerative diseases by analyzing eye movements. The Madrid-based research team and its spin-off company Aura Innovative Robotics have developed a diagnostic test…
…and more accurate outcomes in molecular diagnostics across a wide range of diseases including infectious diseases, neurodegenerative diseases and cancer. It aims to improve lives by providing clarity and accessibility…
…market in Europe Geneuro, for example, is a Swiss company that focuses on diseases of the nervous system and autoimmune diseases. In 2016, it raised €33m (~ $39m) after its…
…therapies for patients with rare diseases. More than 70% of rare diseases are known to be caused by a single mutation, which makes them good candidates for gene therapy. Several…
The European Commission has granted marketing authorization to Ranivisio, a treatment for several serious retinal diseases. Polpharma Biologics Group BV, Formycon AG and their Swiss joint venture, Bioeq AG, announced…
Developing effective treatments for neurological diseases is a big challenge in medicine. But here come UCB and Evotec with a new partnership that could help those suffering from epilepsy and…
…are harnessing the unique biology of tRNAs to engineer a single tRNA medicine that could treat thousands of rare diseases that share the same genetic mutation. This year, Alltrna presented…
…own defective cells. The second is in the broader field of drug discovery. Here, iPS cells are being used to explore the underlying causes of human diseases at a molecular…
Clinical-stage pharmaceutical company, Khondrion, discovering and developing therapies targeting primary mitochondrial diseases announced yesterday (November 22) its wholly-owned lead asset sonlicromanol for MELAS spectrum disorder has demonstrated positive treatment results….
…rare disease, with approximately 3.5 million people in the U.K. affected. With more than 7,000 rare diseases identified, there is a need for new treatments and technologies to speed up…
The Dutch biotech Citryll has raised €15M to develop antibodies that could fight autoimmune and inflammatory diseases more effectively than current treatments by inhibiting the innate immune system. The Series…