…picked some of the rare metabolic diseases, such as urea cycle disorders and those that have no curative therapy and where the standard of care is extremely suboptimal. In all…
…drugs for the treatment of inflammatory and metabolic diseases, such as chronic gout and non-alcoholic steatohepatitis (NASH), for which there are currently no effective treatments. Atom’s lead therapy, known as…
…to address autoimmune conditions without weakening the immune system. The outlook on rare autoimmune diseases As more people are diagnosed with rare autoimmune diseases worldwide, developing new treatments could help…
An international group of researchers has found that the cytokine IL-23 is heavily involved in autoimmune and inflammatory diseases, opening the door to new therapies targeting the molecule. Research at…
…milestone, bringing people with rare genetic diseases one step closer to approved therapies.” Which rare diseases will make the AMP BGTC gene therapy trial portfolio? The eight rare diseases that…
…ultimately blindness continues to increase. While diseases such as wet age-related macular degeneration have seen significant improvements due to the use of VEGF inhibitors, other age-related eye diseases continue to…
…diseases. “The common thread of our approaches to all of these diseases is not splicing but biogenesis of RNA,” CSO Jean-Marc Steens explained to me, though the exact mechanism of…
A food supplement made from bacteria, developed by a Belgian research group, has improved symptoms of the metabolic syndrome including insulin resistance and high blood cholesterol levels in overweight volunteers…
With few options available for the treatment of rare diseases, the practice of drug repurposing has gained traction as an effective strategy. With genome sequencing revealing new rare diseases, it…
…biotech company weathered phase III failures to develop vaccines for neglected diseases. Once confined to the less developed regions of the world, many insect-borne diseases such as Lyme disease and…
…to tackle hard-to-treat diseases. 6 new vaccines being developed for difficult-to-treat diseases (Labiotech.eu) Is a vaccine for Parkinson’s disease possible? (Labiotech.eu) Migraines: a new vaccine frontier beyond infectious diseases (Labiotech.eu)…
…five autoimmune diseases and determine the different inflammatory pathways that can be targeted for the treatment of cancer and autoimmune diseases alike. GIVE ME THE GUIDE! Images via E. Resko…