Mineralys has positive topline results from trial evaluating treatment of hypertension
U.S.-based Mineralys Therapeutics, Inc., announced today (November 16) topline results from its phase 2 Target-HTN…
November 16, 2022 - 4 minutes
Blood disorders
Rallybio announces positive phase 1 results for drug treating PNH and gMG
Affibody’s licensee Rallybio Corporation has announced positive topline results from a phase 1 single ascending…
November 8, 2022 - 3 minutes
Primary Aldosteronism Foundation creates alliance to tackle hypertension
The Primary Aldosteronism Foundation has announced the creation of a multi-stakeholder alliance to drive diagnosis…
September 28, 2022 - 2 minutes
National Hemophilia Foundation launches research fund
The National Hemophilia Foundation (NHF) in the U.S. has announced the launch of Pathway to…
September 22, 2022 - 4 minutes
Gemini Therapeutics and Disc Medicine announce merger agreement
Gemini Therapeutics and Disc Medicine have entered into a definitive merger agreement to combine in…
August 11, 2022 - 2 minutes
Study of drug to treat porphyria disorders initiated by Disc Medicine
A phase 2 clinical study of bitopertin in patients with erythropoietic protoporphyria (EPP) or X-linked…
August 11, 2022 - 3 minutes
Eight diseases CRISPR technology could cure
CRISPR technology offers the promise to cure any human genetic disease with gene editing; which…
October 18, 2021 - 11 minutes
Bluebird Bio Withdrawal Raises Gene Therapy Doubts in Europe
Last month, the US firm bluebird bio abandoned the sale of its gene therapy Zynteglo…
May 4, 2021 - 5 minutes
Bluebird Bio Launches First Gene Therapy for Beta Thalassemia in Germany
The US company bluebird bio has launched the first gene therapy for the blood disorder…
January 14, 2020 - 3 minutes
Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost
The UK gene therapy biotech Freeline Therapeutics is to receive an investment worth €72M (£61.1M)…
December 20, 2019 - 2 minutes
CRISPR Cell Therapy Shows Early Promise for Treating Blood Disorders
CRISPR Therapeutics and its US partner Vertex Pharmaceuticals have released the first clinical results for…
November 19, 2019 - 3 minutes
Orchard’s Gene Therapy Shows Potential in Treating Patients with Beta Thalassemia
Patients with the life-threatening blood disorder beta-thalassemia required fewer blood transfusions after receiving a gene…
April 30, 2019 - 3 minutes
