Blood disorders News, Reviews & Resources

News and Trends 21 Feb 2023

Hemab Therapeutics receives $135M to address bleeding and thrombotic disorders

Hemab Therapeutics, a clinical-stage biotechnology company developing the first prophylactic therapeutics for serious, underserved bleeding and thrombotic disorders, has announced…

February 21, 2023 - 2 minutesmins - By Jim Cornall

News and Trends 14 Feb 2023

Disc Medicine raises $62.5M for hematology programs

Disc Medicine, Inc., a U.S. clinical-stage biopharma company focused on the discovery, development and commercialization of treatments for patients suffering…

February 14, 2023 - 2 minutesmins - By Jim Cornall

Interview 26 Jan 2023

Scopio on the future of telehematology

Through full-field digital cell morphology, Scopio Labs’ technology can automate the analysis of tens of thousands of cells at a…

January 26, 2023 - 4 minutesmins - By Jim Cornall

News and Trends 26 Jan 2023

Milestone for gene-edited therapy for sickle cell disease

Vertex Pharmaceuticals (Europe) and CRISPR Therapeutics have announced that the European Medicines Agency (EMA) has validated the Marketing Authorization Application…

January 26, 2023 - 3 minutesmins - By Jim Cornall

News and Trends 20 Dec 2022

Watch: Sernova’s Cell Pouch System tackles diabetes

Sernova Corp. is a Canadian-based clinical-stage biotechnology company that is developing its Cell Pouch System. This is a novel implantable…

December 20, 2022 - 2 minutesmins - By Jim Cornall

News and Trends 16 Dec 2022

CSL closer to gene therapy treatments for hemophilia B patients in Europe

CSL says the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) has adopted a positive opinion…

December 16, 2022 - 2 minutesmins - By Jim Cornall

News and Trends 13 Dec 2022

Blood clotting research holds hope for sepsis

Researchers from the University of Birmingham in the U.K., who identified a novel mechanism for platelet activation in pathogenic blood…

December 13, 2022 - 2 minutesmins - By Jim Cornall

More News! 16 Nov 2022

Mineralys has positive topline results from trial evaluating treatment of hypertension

U.S.-based Mineralys Therapeutics, Inc., announced today (November 16) topline results from its phase 2 Target-HTN trial in individuals with uncontrolled…

November 16, 2022 - 4 minutesmins - By Liza Laws

News and Trends 8 Nov 2022

Rallybio announces positive phase 1 results for drug treating PNH and gMG

Affibody’s licensee Rallybio Corporation has announced positive topline results from a phase 1 single ascending dose (SAD) study in healthy…

November 8, 2022 - 3 minutesmins - By Jim Cornall

News and Trends 28 Sep 2022

Primary Aldosteronism Foundation creates alliance to tackle hypertension

The Primary Aldosteronism Foundation has announced the creation of a multi-stakeholder alliance to drive diagnosis and treatment of primary aldosteronism,…

September 28, 2022 - 2 minutesmins - By Jim Cornall

News and Trends 22 Sep 2022

National Hemophilia Foundation launches research fund

The National Hemophilia Foundation (NHF) in the U.S. has announced the launch of Pathway to Cures (P2C), a new venture…

September 22, 2022 - 4 minutesmins - By Jim Cornall

News and Trends 11 Aug 2022

Gemini Therapeutics and Disc Medicine announce merger agreement

Gemini Therapeutics and Disc Medicine have entered into a definitive merger agreement to combine in an all-stock transaction. The announcement…

August 11, 2022 - 2 minutesmins - By Liza Laws

News and Trends 11 Aug 2022

Study of drug to treat porphyria disorders initiated by Disc Medicine

A phase 2 clinical study of bitopertin in patients with erythropoietic protoporphyria (EPP) or X-linked protoporphyria (XLP) has been initiated…

August 11, 2022 - 3 minutesmins - By Liza Laws

Best in Biotech 18 Oct 2021

Eight diseases CRISPR technology could cure

CRISPR technology offers the promise to cure any human genetic disease with gene editing; which one will be the first?…

October 18, 2021 - 11 minutesmins - By Clara Rodríguez Fernández

News and Trends 4 May 2021

Bluebird Bio Withdrawal Raises Gene Therapy Doubts in Europe

Last month, the US firm bluebird bio abandoned the sale of its gene therapy Zynteglo in Germany after a pricing…

May 4, 2021 - 5 minutesmins - By Anita Chakraverty

News and Trends 14 Jan 2020

Bluebird Bio Launches First Gene Therapy for Beta Thalassemia in Germany

The US company bluebird bio has launched the first gene therapy for the blood disorder transfusion-dependent beta thalassemia in the…

January 14, 2020 - 3 minutesmins - By Jonathan Smith

News and Trends 20 Dec 2019

Freeline’s Rare Disease Gene Therapies Get €72M Series C Boost

The UK gene therapy biotech Freeline Therapeutics is to receive an investment worth €72M (£61.1M) from the UK VC firm…

December 20, 2019 - 2 minutesmins - By Jonathan Smith

crispr therapeutics vertex beta thalassemia

News and Trends 19 Nov 2019

CRISPR Cell Therapy Shows Early Promise for Treating Blood Disorders

CRISPR Therapeutics and its US partner Vertex Pharmaceuticals have released the first clinical results for a cell therapy made using…

November 19, 2019 - 3 minutesmins - By Jonathan Smith

News and Trends 30 Apr 2019

Orchard’s Gene Therapy Shows Potential in Treating Patients with Beta Thalassemia

Patients with the life-threatening blood disorder beta-thalassemia required fewer blood transfusions after receiving a gene therapy developed by the UK…

April 30, 2019 - 3 minutesmins - By Jonathan Smith

uniQure Freeline aruvant blood disorders

News and Trends 4 Dec 2018

Gene Therapies for Blood Disorders Marching Through the Clinic

Gene therapy holds great potential as a cure for blood disorders such as hemophilia and sickle cell disease, which have…

December 4, 2018 - 3 minutesmins - By Jonathan Smith

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