RNA technology Archives

alnylam silence therapeutics lawsuit settlement

News and Trends 11 Dec 2018

UK Biotech Settles Lawsuit on the First RNAi Drug

Silence Therapeutics and Alnylam have reached a settlement that puts an end to a legal dispute between them resulting in Silence receiving some royalties on Onpattro, the first RNA interference drug. The lawsuit started last year, when Silence went to the UK courts claiming that Alnylam was infringing on its intellectual property. As part of […]

December 11, 2018 - 3 minutesmins - By Clara Rodríguez Fernández

News and Trends 20 Sep 2018

RNA Therapy Shows Promise for Treating Liver Cancer

British biotech MiNA Therapeutics’ innovative RNA treatment may enhance liver cancer patients’ response to standard cancer therapies, suggest early results from a Phase I/IIa clinical trial. When they received the biotech’s small activating RNA (saRNA) treatment, two patients showed complete responses after being given the cancer treatment sorafenib and one showed a partial response to […]

September 20, 2018 - 2 minutesmins - By Jonathan Smith

News and Trends 5 Sep 2018

RNA Therapy Improves Vision in Patients with Rare Genetic Blindness

Dutch company ProQR has released data from a Phase I/II trial showing its RNA therapy can improve the vision of people with a rare form of hereditary blindness. The clinical trial recruited 10 people with the rare disease Leber’s congenital amaurosis 10. Caused by mutations in a gene called CEP290, this condition leads to […]

September 5, 2018 - 2 minutesmins - By Clara Rodríguez Fernández

News and Trends 30 Aug 2018

First RNAi Drug Approved in Europe After 20 Years of Research

The first ever RNA interference (RNAi) drug, used to treat polyneuropathy in patients with hereditary transthyretin-mediated amyloidosis, has been given marketing approval by the European Commision. The approval follows that of the US FDA who gave the green light to US biotech Alnylam Pharmaceutical’s Onpattro (patisiran) earlier this month following positive Phase III findings in […]

August 30, 2018 - 3 minutesmins - By Helen Albert

News and Trends 6 Aug 2018

New Gene Therapy Could Treat Cystic Fibrosis With One Dose

A new partnership in the UK will develop a gene therapy for cystic fibrosis that could treat the disease with a single dose. Cystic fibrosis is a genetic disease that causes mucus to build up in a patient’s lungs. As a result, patients suffer from blocked airways and bacterial infections. While treatment advances have increased […]

August 6, 2018 - 3 minutesmins - By Alexander Burik

Interview 12 Mar 2018

A Dutch Company on the Quest Against Cystic Fibrosis

ProQR is the result of a personal quest against cystic fibrosis started by its CEO, Daniel de Boer. Interested in his story and the company’s unique approach to treating the disease using RNA technology, I decided to speak with him. Daniel de Boer founded ProQR in 2012 following a strong determination to improve the lives […]

March 12, 2018 - 6 minutesmins - By Clara Rodríguez Fernández

News and Trends 6 Mar 2018

French Biotech Uses Natural Peptides to Boost Plant Growth and Immunity

Micropep Technologies, a Toulouse-based biotech, has raised €4M to develop peptides that boost plant growth and disease resistance by regulating gene expression. Micropep Technologies has raised a Series A funding with the support of two new investors, Sofinnova Partners, the largest industrial biotech fund in the world, and Irdi Soridec Gestion. The company aims to use the funding […]

March 6, 2018 - 3 minutesmins - By Alexander Burik

blindness deafness usher syndrome proqr2 1

News and Trends 13 Feb 2018

ProQR Tackles Blindness Caused by a Rare Genetic Disease

ProQR has received €6M from the American charity, Foundation Fighting Blindness, for the development of its treatment for Usher Syndrome – the leading cause of combined blindness and deafness. ProQR focuses on the development of RNA-based medicines for genetic diseases like cystic fibrosis. However, it is the company’s program targeting Usher syndrome, the leading cause of combined […]

February 13, 2018 - 3 minutesmins - By Alex Dale

News and Trends 8 Jan 2018

Galapagos Teams up with Dutch Biotech to Edit Fibrosis out of our RNA

Galapagos and ProQR will work together to target fibrosis using a technology to treat genetic diseases without permanent changes to the DNA. A new research collaboration between two biotech companies in Leiden, the Netherlands, will aim to discover a new class of drugs to treat fibrosis — a process of excessive scarring that leads to […]

January 8, 2018 - 2 minutesmins - By Clara Rodríguez Fernández

Best in Biotech 18 Dec 2017

Smile! Here are the 12 Biggest Biotech Clinical Successes of 2017

Now that we’ve got the bad news out of the way, we’re here to spread some Christmas cheer with the biggest clinical successes in biotech over the past 12 months. It’s unlikely that one whole year will ever pass without a single hiccup, especially in a field as complex as biotech. For that reason, we […]

December 18, 2017 - 9 minutesmins - By Alex Dale

dystrophic epidermolysis bullosa proqr rna therapy

News and Trends 30 Nov 2017

RNA Therapy for Rare Skin Disease Gets Orphan Status

The EMA has granted orphan drug designation to ProQR’s QR-313, a possible first disease-modifying treatment for the rare disease dystrophic epidermolysis bullosa. Dystrophic epidermolysis bullosa (DEB) is a genetic disease that causes the skin to easily blister, severely affecting the quality of life of patients since a very early age. Current treatment is limited to […]

November 30, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

Infographics 22 Nov 2017

Infographic: What is RNAi Therapy? Targeting the Untargetable

Everything you need to know about what RNAi is, how it works and how it could soon change the way we treat all sorts of diseases. A new wave of therapies based on RNA interference is on the brink of making it to the market. A technology that was awarded the Nobel prize in 2006, […]

November 22, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

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RNA technology

UK Biotech Settles Lawsuit on the First RNAi Drug

RNA Therapy Shows Promise for Treating Liver Cancer

RNA Therapy Improves Vision in Patients with Rare Genetic Blindness

First RNAi Drug Approved in Europe After 20 Years of Research

New Gene Therapy Could Treat Cystic Fibrosis With One Dose

A Dutch Company on the Quest Against Cystic Fibrosis

French Biotech Uses Natural Peptides to Boost Plant Growth and Immunity

ProQR Tackles Blindness Caused by a Rare Genetic Disease

Galapagos Teams up with Dutch Biotech to Edit Fibrosis out of our RNA

Smile! Here are the 12 Biggest Biotech Clinical Successes of 2017

RNA Therapy for Rare Skin Disease Gets Orphan Status

Infographic: What is RNAi Therapy? Targeting the Untargetable

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Catalonia: A biotech hub going from strength to strength, with Barcelona at its core

Top biotech deals of February 2025

Grab your free report on 3D organoids and explore their future potential

These 7 biotechs are shaping the next generation of endometriosis care

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

Catalonia: A biotech hub going from strength to strength, with Barcelona at its core

Top biotech deals of February 2025

Grab your free report on 3D organoids and explore their future potential

These 7 biotechs are shaping the next generation of endometriosis care

Connect with decision-makers and researchers worldwide for collaborative opportunities

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Advertise with us

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