News and Trends 1 Jun 2016
EMA approves Groundbreaking Gene Therapy for Super Rare ‘Bubble Baby’ Disease
GSK, Fondazione Telethon and Ospedale San Raffaele have announced that the EMA has approved Strimvelis for a super rare immunodeficiency disease in Children. Following 20 years of research at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget) in Italy, this is the news patients have been waiting for. Strimvelis is the first ex vivo stem cell gene […]