News and Trends 25 Feb 2019
Orchard Achieves Good Survival with Cell Therapy for Rare Immune Deficiency
All 20 patients with a rare immunodeficiency disease survived for at least two years after receiving a cell therapy developed by Orchard Therapeutics. The patients had a genetic disease called adenosine deaminase–deficient severe combined immune deficiency (ADA-SCID) — also known as bubble boy syndrome. Caused by a mutation on a vital gene, the disease weakens […]
