News and Trends 7 Dec 2018
Orchard’s Gene Therapy for Rare Immune Disease Works for Over a Year
A single dose of a gene therapy developed by Orchard Therapeutics can restore immune function for at least a year in patients with X-linked chronic granulomatous disease (X-CGD). The gene therapy was trialed in patients between the ages of 2 and 27 with the rare disease, which is caused by a rare genetic mutation that […]
