Gene therapy Archives

News and Trends 18 Sep 2018

Update: French Biotech Raises €22M for a Gene Therapy Trial in Retinitis Pigmentosa

Update (18/09/2018): Horama has increased the total raised in its Series B fundraising to €22.5M, with the Belgian fund V-Bio Ventures joining the team of investors backing the company. The funds will be mainly directed at developing Horama’s gene therapy for retinitis pigmentosa. Published on 08/10/2017 Horama has raised a second fundraising round that will support […]

September 18, 2018 - 2 minutesmins - By Clara Rodríguez Fernández

News and Trends 13 Aug 2018

Orchard Therapeutics Raises €132M to Develop Gene Therapies

Orchard Therapeutics raised $150M (€132M) in Series C financing to bring its gene therapies from clinical testing to regulatory approval. The British biotech will use the funding to develop its most advanced clinical programs, which aim to treat rare inherited metabolic and immune system diseases. The news follows Orchard’s acquisition of GSK’s entire gene therapy […]

August 13, 2018 - 2 minutesmins - By Alexander Burik

News and Trends 10 Aug 2018

UK Biotech Raises €73M to Target DNA Repair in Treating Cancer

Artios Pharma completed a €73M (£65M) Series B financing round to develop cancer treatments that target DNA repair mechanisms. Cancer occurs when cells in part of the body start dividing uncontrollably as a result of damaged or mutated DNA. In collaboration with Cancer Research UK, Artios Pharma is developing cancer treatments that inhibit proteins involved […]

August 10, 2018 - 3 minutesmins - By Alexander Burik

News and Trends 6 Aug 2018

New Gene Therapy Could Treat Cystic Fibrosis With One Dose

A new partnership in the UK will develop a gene therapy for cystic fibrosis that could treat the disease with a single dose. Cystic fibrosis is a genetic disease that causes mucus to build up in a patient’s lungs. As a result, patients suffer from blocked airways and bacterial infections. While treatment advances have increased […]

August 6, 2018 - 3 minutesmins - By Alexander Burik

More News! 2 Aug 2018

Tomato DNA Could Help Uncover Counterfeit Breast Implants

Counterfeit breast implants can harm patients’ health and even threaten their lives. A German research team is using tomato DNA tags to tell the ‘real thing’ apart from frauds. The silicone used in implants need to have a high-quality to prevent silicone from leaking out of the implant. As a result, the silicone used in […]

August 2, 2018 - 2 minutesmins - By Alexander Burik

News and Trends 17 Jul 2018

Gene Therapy Could Prevent Deadly Brain Disease

An international research team used gene therapy to prevent Gaucher disease, a potentially deadly neurodegenerative condition, in mice. The approach could eventually be used to treat human diseases in the womb. A research team from the UK and Singapore showed that a neurodegenerative condition called Gaucher disease, which can be fatal, can be prevented in […]

July 17, 2018 - 3 minutesmins - By Alexander Burik

Retinitis pigmentosa gene therapy Horama

News and Trends 11 Jul 2018

Gene Therapy for Retinitis Pigmentosa Tested in Humans for the First Time

French biotech Horama has treated the first patients with a gene therapy for retinitis pigmentosa that could prevent the progressive loss of vision caused by this genetic condition. A Phase I/II trial with Horama’s gene therapy for retinitis pigmentosa is running at the Nantes University Hospital. The therapy is aimed at fixing genetic defects in a […]

July 11, 2018 - 3 minutesmins - By Clara Rodríguez Fernández

News and Trends 6 Jun 2018

German DNA Treatment Reduces Ulcerative Colitis Symptoms

Sterna Biologicals has obtained positive Phase IIa data for an ulcerative colitis treatment that uses DNA to inhibit inflammatory proteins, which could add to the diverse approaches being developed to treat inflammatory bowel disease. Sterna Biologicals, based in Marburg, Germany, has clinical data showing its ulcerative colitis treatment reduced the severity of the disease compared […]

June 6, 2018 - 3 minutesmins - By Alexander Burik

News and Trends 3 May 2018

FDA Backs Gene Therapy for Fatal Neurodegenerative Childhood Disease

Orchard Therapeutics has received a fourth Rare Pediatric Disease Designation from the FDA for its gene therapy candidate for metachromatic leukodystrophy. Orchard Therapeutics, based in London, has received a Rare Pediatric Disease Designation form the FDA for its gene therapy OTL-200. The treatment is for patients with metachromatic leukodystrophy (MLD), a fatal genetic disease that causes […]

May 3, 2018 - 1 minutemin - By Alexander Burik

News and Trends 3 May 2018

World’s First Gene Therapy Developer Raises $128M for Hemophilia and Huntington’s

uniQure has raised a substantial public offering on the NASDAQ. The funding could help the Dutch biotech advance two new gene therapies after the withdrawal of its first treatment. Amsterdam-based uniQure has raised an ambitious $128M (€107M) in a public offering at the beginning of next week. The Dutch biotech develops gene therapies for hemophilia and Huntington’s disease, for […]

May 3, 2018 - 2 minutesmins - By Alexander Burik

News and Trends 25 Apr 2018

Cancer Treatment Targeting DNA Repair is Tested in Humans for the First Time

Onxeo has initiated a Phase I trial testing its first-in-class cancer treatment that works by inhibiting the repair of tumor DNA. Onxeo, a French biotech, has dosed its first patient in a Phase I study testing its cancer treatment AsiDNA, the first treatment of its kind, for advanced solid tumors. The news follows the Phase […]

April 25, 2018 - 1 minutemin - By Alexander Burik

News and Trends 20 Apr 2018

Gene Therapy For Beta-Thalassemia Could Eliminate Need for Transfusions

Bluebird bio has obtained results from two clinical studies showing its new gene therapy could eliminate the need for red blood cell transfusions in patients with beta-thalassemia. The company plans to file for an EU approval of its treatment later this year. US firm bluebird bio has results from two clinical studies showing its LentiGlobin gene […]

April 20, 2018 - 2 minutesmins - By Alexander Burik

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Gene therapy

Update: French Biotech Raises €22M for a Gene Therapy Trial in Retinitis Pigmentosa

Orchard Therapeutics Raises €132M to Develop Gene Therapies

UK Biotech Raises €73M to Target DNA Repair in Treating Cancer

New Gene Therapy Could Treat Cystic Fibrosis With One Dose

Tomato DNA Could Help Uncover Counterfeit Breast Implants

Gene Therapy Could Prevent Deadly Brain Disease

Gene Therapy for Retinitis Pigmentosa Tested in Humans for the First Time

German DNA Treatment Reduces Ulcerative Colitis Symptoms

FDA Backs Gene Therapy for Fatal Neurodegenerative Childhood Disease

World’s First Gene Therapy Developer Raises $128M for Hemophilia and Huntington’s

Cancer Treatment Targeting DNA Repair is Tested in Humans for the First Time

Gene Therapy For Beta-Thalassemia Could Eliminate Need for Transfusions

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Illuminating biotech in the City of Light: Inside Paris’s thriving ecosystem

ASCO 2025: key highlights in cancer therapeutics

New report: Artificial intelligence and the future of antibody discovery

Stem cell therapy: a potential cure for hearing loss?

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

Illuminating biotech in the City of Light: Inside Paris’s thriving ecosystem

ASCO 2025: key highlights in cancer therapeutics

New report: Artificial intelligence and the future of antibody discovery

Stem cell therapy: a potential cure for hearing loss?

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

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