Gene therapy Archives

News and Trends 25 Apr 2017

EMA designates uniQure’s gene therapy for hemophilia a priority

Following a Breakthrough Designation from the FDA earlier this year, the Dutch biotech has scored the European equivalent for AMT-060. Since its claim to fame, Glybera, fell from grace to become a commercial failure, uniQure has been on the rebound. The company recently has undergone several management shakeups and a strategy review, and it just made the decision to withdraw […]

April 25, 2017 - 3 minutesmins - By Evelyn Warner

SIRION Biotech cell therapy lentivirus lentiboost

News and Trends 12 Apr 2017

Taking Cell Therapy one Step Further with this Boost Reagent

Cell therapy is revolutionizing medicine, here’s how the latest technology can help overcome the major challenges stopping it from taking over the market. Offering unprecedented possibilities to treat some of the most challenging diseases, cell therapy is stealing the show in the biotech space. Strimvelis, the first hematopoietic stem cell (HSC) gene therapy is already […]

April 12, 2017 - 4 minutesmins - By External Contributor

Eyevensis Eye Gene Therapy Approval France

News and Trends 11 Apr 2017

France Approves Trials for the First Eye Gene Therapy Free of Viral DNA

Eyevensys has received regulatory approval in France to start clinical trials using eye gene therapy technology that eliminates the need for viral vectors. The French biotech Eyevensys has been cleared by the French Product Security Regulatory Agency (ANSM) to proceed into the clinic with its EyeCET platform. The company is developing this gene therapy platform […]

April 11, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

Interview 3 Apr 2017

Meet the Co-Founder who says DNA is the Next Silicon

DNA Script opens the door to a whole new age of manufacturing synthetic DNA. Thomas Ybert, was only 30 when he co-founded the company – here’s his story! Based in Paris, DNA Script produces synthetic DNA using a proprietary template-free enzymatic technology. Most of the manufactured DNA is currently synthesized by chemical means, but this startup […]

April 3, 2017 - 5 minutesmins - By External Contributor

Lysogene gene therapy Sanfillipo A obs study

News and Trends 29 Mar 2017

French Gene Therapy Biotech Gets Ready for Phase II/III

Lysogene has crunched the numbers on its observational study for Sanfillipo A – now the company can move into the final phase for its Sanfilippo A therapy. Lysogene is a French biotech specializing in gene therapy of rare CNS diseases. Its lead asset is a gene therapy for the treatment of the rare genetic disorder […]

March 29, 2017 - 3 minutesmins - By Melanie De Almeida

News and Trends 28 Mar 2017

Why did Biotech Beat Pharma to Bring the First Gene Therapy to Market?

Pharma would seemingly best biotech in any competition. A few CEOs explain why it left the honor of “The First Gene Therapy” to biotech. On July 20, 2012, the western world’s first gene therapy, Glybera, received marketing authorization from the EMA. The treatment was designed and developed by uniQure as one-off treatment for Lipoprotein Lipase Deficiency (LPLD), a […]

March 28, 2017 - 5 minutesmins - By Evelyn Warner

News and Trends 14 Mar 2017

The First 3D Structure of Active DNA could advance Stem Cell Therapies

Scientists from the University of Cambridge have determined the first 3D structures of mammalian genomes from individual cells. For the first time, researchers from the University of Cambridge were able to determine the 3D structure of an active mouse genome in embryonic stem cells. Tim Stevens and his colleagues used a combination of imaging and […]

March 14, 2017 - 3 minutesmins - By Melanie De Almeida

News and Trends 28 Feb 2017

It’s Global Rare Disease Day! What Cures is Biotech Cooking Up?

We’ve compiled a list of some of the latest advances of biotech in the field of rare disease to contribute to Rare Disease Day 2017. The European Organization for Rare Diseases (EURORDIS) is once again coordinating Rare Disease Day, which takes place on the last day of February every year. The aim is to raise awareness of […]

February 28, 2017 - 5 minutesmins - By Clara Rodríguez Fernández

Arthrogen rheumatoid arthritis gene therapy

News and Trends 17 Feb 2017

Gene Therapy for Rheumatoid Arthritis gets Approval to Start Clinical Trials

Arthrogen will start a Phase Ib trial for a gene therapy aiming to treat rheumatoid arthritis with a single injection and reduce costs for patients. Arthrogen, based in Amsterdam, is developing local gene therapies for inflammatory diseases. The biotech company has now announced it has received approval to start a Phase Ib trial with its lead […]

February 17, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

News and Trends 17 Feb 2017

UPDATE: More Promising Results from Mologen’s New HIV Therapy

Update (17/02/2017): Mologen has announced more positive data for lefitolimod in HIV, as the Danish Aarhus University Hospital showed for the first time that the drug can induce a local antiviral immune response in patients undergoing ART. Definitive results are expected later this year. Originally published on 11/01/2017 Mologen’s partner in the development of an HIV therapy has […]

February 17, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

News and Trends 15 Feb 2017

Optogenetics: What Makes It a Powerful Neuroscience Tool?

It’s a brand-new field and possibilities seem infinite. Here’s what you need to know about its rapid development into a powerful genetic tool. What is Optogenetics? What if you could activate and deactivate neurons by simply switching on the lights? That’s the basis of optogenetics, the control of cell behavior via light-sensitive proteins. Optogenetics is a […]

February 15, 2017 - 3 minutesmins - By External Contributor

lysogene ipo euronext paris e1486638993948

News and Trends 9 Feb 2017

Gene Therapy Biotech Founded to Save the CEO’s Daughter Goes Public in France

Lysogene has raised €22.6M from its IPO on Euronext Paris that will contribute to the completion of clinical trials to treat the rare genetic diseases. Karen Aiach, CEO of Lysogene, started the company back in 2009 to develop a life-saving treatment for her daughter Ornella with Sanfilippo A. This rare genetic disease severely affects the nervous system of […]

February 9, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

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Gene therapy

EMA designates uniQure’s gene therapy for hemophilia a priority

Taking Cell Therapy one Step Further with this Boost Reagent

France Approves Trials for the First Eye Gene Therapy Free of Viral DNA

Meet the Co-Founder who says DNA is the Next Silicon

French Gene Therapy Biotech Gets Ready for Phase II/III

Why did Biotech Beat Pharma to Bring the First Gene Therapy to Market?

The First 3D Structure of Active DNA could advance Stem Cell Therapies

It’s Global Rare Disease Day! What Cures is Biotech Cooking Up?

Gene Therapy for Rheumatoid Arthritis gets Approval to Start Clinical Trials

UPDATE: More Promising Results from Mologen’s New HIV Therapy

Optogenetics: What Makes It a Powerful Neuroscience Tool?

Gene Therapy Biotech Founded to Save the CEO’s Daughter Goes Public in France

Subscribe to our newsletter to get the latest biotech news!

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

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