Gene therapy Archives

GeneSight eye gene therapy sight restoration

News and Trends 5 Dec 2017

Update: French Gene Therapy Yields Longer Term Sight Restoration, Eyes Phase III

Update (05/12/2017): GenSight has reported a sustained effect of its treatment GS010, which has now been shown to restore sight in patients for at least 2.5 years after administration. Phase III results for the candidate are expected next year. Originally published 14/06/2017 GenSight has announced Phase I/II data revealing that its gene therapy technology can […]

December 5, 2017 - 3 minutesmins - By Clara Rodríguez Fernández

Interview 4 Dec 2017

Meet the CEO Leading Italy’s Charge to Become a Major Biotech Player

Riccardo Palmisano is CEO of MolMed, the most important Italian biotech, which focuses on gene and cell therapies. We chatted about the company, which hopes to give the cancer therapies field a boost. You may have come across MolMed before, possibly in our recent piece on the top biotechs in Milan. The company was founded […]

December 4, 2017 - 7 minutesmins - By Alex Dale

News and Trends 28 Nov 2017

Cheap DNA Tests for Everyone! Italian Biotech Launches €149 Kit

Dante Labs has developed the first DNA tests available in Europe, which will allow the public to test their health and wellbeing from the comfort of their own homes. Dante Labs hopes to transform genetics. The biotech wants to develop accessible genomic testing, giving people the knowledge and information they need to live long, healthy lives. Yesterday, the […]

November 28, 2017 - 3 minutesmins - By Alex Dale

News and Trends 28 Nov 2017

New Gene Therapy for Parkinson’s will be Developed in the UK

Synpromics and UCL will collaborate to develop a gene therapy to treat Parkinson’s disease that only targets specific neurons involved in the disease. Synpromics, based in Edinburgh, Scotland, is a company focusing on gene control. The biotech has decided to put its technology to use for the development of a gene therapy for Parkinson’s in […]

November 28, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

In Depth 28 Nov 2017

Reviewing Gene Therapy: How Close is Biotech to Genetic Cures?

Over 10,000 human diseases are caused by exactly one faulty gene. Gene therapy promises to fix each of them. Here’s a review of biotech’s progress. Biotech is arguably built on genetic medicine. When Genentech‘s insulin produced by genetically engineered bacteria kicked off biotech fever in the 1980s, the concept of directly repairing defective human DNA wasn’t […]

November 28, 2017 - 8 minutesmins - By Evelyn Warner

In Depth 23 Nov 2017

The Future is (Syn)Bio: How and when do we get there?

Last week, Philip and I attended a meeting with some of the pioneers and leaders of the synthetic biology field. They believe biology will be everywhere in the future, but how do we get ready for it? Digital technologies are now present in almost all aspects of our lives. It seems obvious today that companies […]

November 23, 2017 - 5 minutesmins - By Clara Rodríguez Fernández

News and Trends 2 Nov 2017

Close to Launching Gene Therapy, Dutch Biotech Raises Over $91M on the Nasdaq

Update (2/11/2017): uniQure has closed its public offering raising over $91m (€78M) on the Nasdaq, taking advantage of a massive stock jump triggered by the announcement that an improved version of its gene therapy for hemophilia B will enter Phase III trials. Originally published on 24/10/2017 UniQure launched a public offering, perfectly timed with a rise in […]

November 2, 2017 - 3 minutesmins - By Clara Rodríguez Fernández

News and Trends 19 Oct 2017

Dutch Biotech plans Pivotal Clinical Trial with First Gene Therapy for Hemophilia

uniQure is getting ready to start a Phase III clinical trial in 2018 with a new version of its gene therapy for hemophilia B. uniQure has officially launched a plan to bring the first gene therapy for hemophilia to the market. After multiple meetings with the FDA and the EMA, the Dutch biotech has received permission […]

October 19, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

News and Trends 11 Oct 2017

French Gene Therapy to Cure Retinitis Pigmentosa Enters the Clinic

Horama has been authorized to start a Phase I/II trial in France testing HORA-PDE6B, a one-off gene therapy with the potential to cure retinitis pigmentosa. Based in Paris, Horama develops gene therapies to treat genetic diseases affecting vision. The company will now start a Phase I/II clinical trial that will recruit 12 patients at the Nantes […]

October 11, 2017 - 3 minutesmins - By Clara Rodríguez Fernández

News and Trends 6 Oct 2017

British-Finnish Alliance to Bring Gene Therapy to the Masses

FIT Biotech and Avacta hope to combine their technologies to produce highly specific, best-in-class gene therapy treatments. The two companies have spotted an opportunity to bring together their technologies and form a leading gene therapy system in a market that could be worth over $4.3B (€3.7B) by 2024. FIT Biotech, based in Finland, has been working on […]

October 6, 2017 - 2 minutesmins - By Alex Dale

News and Trends 28 Sep 2017

Oxford Spinout goes for $75M IPO on Nasdaq to Fund Gene Therapy Programs

Nightstar has gone public on the American market with the aim of raising $75M for its gene-based retinal disease cures. Spun out from Oxford in 2013, Nightstar is developing and commercializing one-shot gene therapies for various eye diseases that could lead to blindness. This morning, it debuted on the Nasdaq with a projected $75M (£56M / €64M) […]

September 28, 2017 - 2 minutesmins - By Evelyn Warner

News and Trends 27 Sep 2017

French Gene Therapy for Wilson’s Disease gets Orphan Status

Vivet Therapeutics has been granted Orphan Drug Designation for its gene therapy for Wilson’s disease, VTX-801, by both the FDA and the European Commission. The French biotech Vivet Therapeutics is developing what could eventually become the first gene therapy for Wilson’s disease. Seeing its potential, both the FDA and the EC have decided to grant […]

September 27, 2017 - 2 minutesmins - By Clara Rodríguez Fernández

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Gene therapy

Update: French Gene Therapy Yields Longer Term Sight Restoration, Eyes Phase III

Meet the CEO Leading Italy’s Charge to Become a Major Biotech Player

Cheap DNA Tests for Everyone! Italian Biotech Launches €149 Kit

New Gene Therapy for Parkinson’s will be Developed in the UK

Reviewing Gene Therapy: How Close is Biotech to Genetic Cures?

The Future is (Syn)Bio: How and when do we get there?

Close to Launching Gene Therapy, Dutch Biotech Raises Over $91M on the Nasdaq

Dutch Biotech plans Pivotal Clinical Trial with First Gene Therapy for Hemophilia

French Gene Therapy to Cure Retinitis Pigmentosa Enters the Clinic

British-Finnish Alliance to Bring Gene Therapy to the Masses

Oxford Spinout goes for $75M IPO on Nasdaq to Fund Gene Therapy Programs

French Gene Therapy for Wilson’s Disease gets Orphan Status

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The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

The top biotech deals of March 2025

The biggest biotech funding rounds in March 2025

Join the webinar: AI in antibody discovery - from in silico analysis to AI-enabled data management

Beyond amyloid: The search for the next big thing in Alzheimer’s treatment

Connect with decision-makers and researchers worldwide for collaborative opportunities

Subscribe to our newsletter

Advertise with us

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